Malan overgrowth syndrome

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:420179OMIM:614753Q87.3
Who is this for?
Show terms as
8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Malan overgrowth syndrome (also called Sotos syndrome 2 or NFIX-related overgrowth syndrome) is a rare genetic condition that causes children to grow faster and larger than expected, both in body size and head size. It is caused by changes in a gene called NFIX, which plays an important role in how the brain and body develop before and after birth. The syndrome was first described by Dr. Alain Malan and colleagues and is recognized as a distinct condition from the more well-known Sotos syndrome, though the two share many features. Children with Malan syndrome typically have a tall stature, a larger-than-average head (macrocephaly), and distinctive facial features such as a long face, widely spaced eyes, and a prominent forehead. Most children also experience some degree of intellectual disability, ranging from mild to moderate, along with delayed speech and language development. Behavioral challenges, including anxiety, attention difficulties, and sometimes features of autism spectrum disorder, are also common. There is currently no cure for Malan syndrome. Treatment focuses on supporting each child's individual needs through speech therapy, occupational therapy, physical therapy, and educational support. Regular monitoring by a team of specialists helps manage symptoms and improve quality of life. With the right support, many individuals with Malan syndrome can make meaningful developmental progress.

Also known as:

Key symptoms:

Faster than normal growth in height and body size (overgrowth)Larger than average head size (macrocephaly)Intellectual disability, usually mild to moderateDelayed speech and language developmentDelayed motor milestones such as sitting and walkingDistinctive facial features including a long face, prominent forehead, and widely spaced eyesBehavioral challenges such as anxiety or attention difficultiesFeatures of autism spectrum disorder in some individualsLow muscle tone (hypotonia) in infancyFeeding difficulties in early infancyTall stature compared to peersLearning difficulties at school age

Clinical phenotype terms (38)— hover any for plain English
Oval faceHP:0000300Slender long boneHP:0003100
Inheritance

Autosomal dominant

Passed on from just one parent; each child has about a 50% chance of inheriting it

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Malan overgrowth syndrome.

View clinical trials →

No actively recruiting trials found for Malan overgrowth syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Malan overgrowth syndrome community →

No specialists are currently listed for Malan overgrowth syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Malan overgrowth syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Malan overgrowth syndromeForum →

No community posts yet. Be the first to share your experience with Malan overgrowth syndrome.

Start the conversation →

Latest news about Malan overgrowth syndrome

No recent news articles for Malan overgrowth syndrome.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What therapies should my child start right away, and how often should they attend?,Should we do any additional tests, such as brain MRI or heart evaluation?,What behavioral or emotional challenges should I watch for as my child grows?,How do I get an individualized education plan (IEP) set up for my child at school?,Are there any clinical trials or research studies we could participate in?,What does the long-term outlook look like for my child in terms of independence and daily living?,Should other family members be tested for changes in the NFIX gene?

Common questions about Malan overgrowth syndrome

What is Malan overgrowth syndrome?

Malan overgrowth syndrome (also called Sotos syndrome 2 or NFIX-related overgrowth syndrome) is a rare genetic condition that causes children to grow faster and larger than expected, both in body size and head size. It is caused by changes in a gene called NFIX, which plays an important role in how the brain and body develop before and after birth. The syndrome was first described by Dr. Alain Malan and colleagues and is recognized as a distinct condition from the more well-known Sotos syndrome, though the two share many features. Children with Malan syndrome typically have a tall stature, a

How is Malan overgrowth syndrome inherited?

Malan overgrowth syndrome follows a autosomal dominant inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Malan overgrowth syndrome typically begin?

Typical onset of Malan overgrowth syndrome is neonatal. Age of onset can vary across affected individuals.