Tatton-Brown-Rahman syndrome

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ORPHA:404443OMIM:615879Q87.3
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8Treatment centers

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Overview

Tatton-Brown-Rahman syndrome (TBRS), also known as DNMT3A overgrowth syndrome, is a rare genetic condition caused by changes (mutations) in the DNMT3A gene. This gene plays an important role in how the body controls gene activity through a process called DNA methylation. When this gene does not work properly, it leads to a pattern of overgrowth, intellectual disability, and distinctive facial features. Children with TBRS are often taller and heavier than expected from birth or early childhood. They typically have a larger-than-average head size (macrocephaly) and may show mild to moderate intellectual disability or learning difficulties. Facial features can include a round face, heavy eyebrows, and widely spaced eyes. Some individuals may also develop obesity and joint hypermobility (unusually flexible joints). Behavioral challenges, including features of autism spectrum disorder, have been reported in some patients. There is currently no cure for Tatton-Brown-Rahman syndrome. Treatment focuses on managing individual symptoms and supporting development. This includes early intervention programs, speech therapy, occupational therapy, and educational support. Regular monitoring by a team of specialists helps address the various aspects of the condition as the child grows. The syndrome was first described in 2014, and researchers continue to learn more about it, meaning care recommendations may evolve over time.

Also known as:

Key symptoms:

Tall stature or overgrowth from early childhoodLarger-than-average head sizeIntellectual disability, usually mild to moderateLearning difficultiesRound face with distinctive facial featuresHeavy or thick eyebrowsWidely spaced eyesObesity or increased weightUnusually flexible joints (joint hypermobility)Low muscle tone in infancySpeech and language delaysBehavioral challengesFeatures of autism spectrum disorderDifficulty with fine motor skillsScoliosis or other skeletal differences

Clinical phenotype terms (40)— hover any for plain English
Proportionate tall statureHP:0011407Widely-spaced maxillary central incisorsHP:0001566Chiari malformationHP:0002308
Inheritance

Autosomal dominant

Passed on from just one parent; each child has about a 50% chance of inheriting it

Age of Onset

Childhood

Begins in childhood, roughly ages 1 to 12

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Tatton-Brown-Rahman syndrome.

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No actively recruiting trials found for Tatton-Brown-Rahman syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Tatton-Brown-Rahman syndrome community →

No specialists are currently listed for Tatton-Brown-Rahman syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Tatton-Brown-Rahman syndrome.

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Community

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Latest news about Tatton-Brown-Rahman syndrome

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What specific DNMT3A mutation does my child have, and does it tell us anything about what to expect?,What therapies should we start right away to support my child's development?,How often should my child have growth and developmental check-ups?,Is there any increased risk of cancer or other serious health problems we should monitor for?,Should other family members be tested for the DNMT3A mutation?,What educational supports and accommodations should we request at school?,Are there any clinical trials or research studies we could participate in?

Common questions about Tatton-Brown-Rahman syndrome

What is Tatton-Brown-Rahman syndrome?

Tatton-Brown-Rahman syndrome (TBRS), also known as DNMT3A overgrowth syndrome, is a rare genetic condition caused by changes (mutations) in the DNMT3A gene. This gene plays an important role in how the body controls gene activity through a process called DNA methylation. When this gene does not work properly, it leads to a pattern of overgrowth, intellectual disability, and distinctive facial features. Children with TBRS are often taller and heavier than expected from birth or early childhood. They typically have a larger-than-average head size (macrocephaly) and may show mild to moderate int

How is Tatton-Brown-Rahman syndrome inherited?

Tatton-Brown-Rahman syndrome follows a autosomal dominant inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Tatton-Brown-Rahman syndrome typically begin?

Typical onset of Tatton-Brown-Rahman syndrome is childhood. Age of onset can vary across affected individuals.