Goblet cell carcinoma

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3Specialists8Treatment centers

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Overview

Goblet cell carcinoma (also called goblet cell adenocarcinoma, or previously goblet cell carcinoid) is a rare type of cancer that most commonly arises in the appendix. It gets its name from the goblet-shaped cells that are normally found lining the intestines and produce mucus. This cancer is unique because it has features of both a carcinoid (neuroendocrine) tumor and a traditional adenocarcinoma, making it a mixed or hybrid tumor type. It tends to behave more aggressively than typical carcinoid tumors of the appendix. Patients with goblet cell carcinoma may initially have no symptoms at all, and the tumor is sometimes discovered incidentally during surgery for what appears to be appendicitis. When symptoms do occur, they can include abdominal pain (often in the lower right side), bloating, changes in bowel habits, and sometimes a palpable mass. In more advanced cases, the cancer can spread to nearby organs such as the ovaries, peritoneum (the lining of the abdomen), and other parts of the intestines. Treatment typically involves surgery, which may range from a simple appendectomy to a right hemicolectomy (removal of part of the colon) depending on the stage and grade of the tumor. In cases where the cancer has spread, chemotherapy is often recommended, usually with regimens similar to those used for colorectal cancer. Because this cancer is rare, treatment decisions are often made by multidisciplinary teams at specialized cancer centers. Outcomes vary widely depending on the stage at diagnosis, with early-stage disease having a much better prognosis than advanced disease.

Also known as:

Key symptoms:

Abdominal pain, especially in the lower right sideSymptoms mimicking appendicitisBloating or abdominal swellingChanges in bowel habitsNausea or vomitingUnexplained weight lossA lump or mass felt in the abdomenPelvic pain or pressureOvarian masses in women (from cancer spread)Loss of appetiteFatigueBowel obstruction symptoms

Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Adult

Begins in adulthood (age 18 or older)

Orphanet ↗NORD ↗

FDA & Trial Timeline

6 events
Apr 2026GCC 2546- Motion Management

University of Maryland, Baltimore — NA

TrialNOT YET RECRUITING
May 2025Autologous CAR-T Cells (WD-01) for Metastatic Colorectal Cancer

Wondercel Biotech (ShenZhen) — EARLY_PHASE1

TrialRECRUITING
Mar 2023Neoadjuvant Immunotherapy of Operable Metastatic Melanoma in Real Life (GCC)

Centre Hospitalier Universitaire de Besancon

TrialRECRUITING
Nov 2022GCC Agonist Signal in the Small Intestine

University of Wisconsin, Madison — PHASE1

TrialACTIVE NOT RECRUITING
Sep 2021GammaPod Dose Escalation Radiation for Early Stage Breast Cancer

University of Maryland, Baltimore — NA

TrialRECRUITING
Nov 2020Hypofractionated Accelerated Pelvic Nodal Radiotherapy (GCC 2048)

University of Maryland, Baltimore — PHASE1

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Goblet cell carcinoma.

View clinical trials →

No actively recruiting trials found for Goblet cell carcinoma at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Goblet cell carcinoma community →

Specialists

3 foundView all specialists →
LS
Lin Shen
Specialist
PI on 7 active trials110 Goblet cell carcinoma publications
EV
Eduardo Vilar-Sanchez
Duarte, California
Specialist

Rare Disease Specialist

PI on 3 active trials
KM
Katherine Tkaczuk, MD
BALTIMORE, MD
Specialist
PI on 3 active trials

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Goblet cell carcinoma.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Goblet cell carcinomaForum →

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Latest news about Goblet cell carcinoma

Disease timeline:

New recruiting trial: Hypofractionated Accelerated Pelvic Nodal Radiotherapy (GCC 2048)

A new clinical trial is recruiting patients for Goblet cell carcinoma

New recruiting trial: LITT Followed by Hypofractionated RT for Newly Diagnosed Gliomas (GCC 20138)

A new clinical trial is recruiting patients for Goblet cell carcinoma

New recruiting trial: Neoadjuvant Immunotherapy of Operable Metastatic Melanoma in Real Life (GCC)

A new clinical trial is recruiting patients for Goblet cell carcinoma

New recruiting trial: GammaPod Dose Escalation Radiation for Early Stage Breast Cancer

A new clinical trial is recruiting patients for Goblet cell carcinoma

New recruiting trial: Autologous CAR-T Cells (WD-01) for Metastatic Colorectal Cancer

A new clinical trial is recruiting patients for Goblet cell carcinoma

New trial: Cancer Preventive Vaccine Nous-209 for Lynch Syndrome Patients

Phase PHASE1 trial recruiting. Adenoviral Tumor-specific Neoantigen Priming Vaccine GAd-209-FSP

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What is the exact stage and grade of my goblet cell carcinoma, and what does that mean for my outlook?,Do I need additional surgery beyond the appendectomy, such as a right hemicolectomy?,Should I be referred to a specialized center that offers cytoreductive surgery and HIPEC?,Is chemotherapy recommended in my case, and what regimen would you suggest?,For women: Should I consider removal of my ovaries to prevent spread to that area?,How often will I need follow-up scans and blood tests, and for how long?,Are there any clinical trials available for goblet cell carcinoma that I might be eligible for?

Common questions about Goblet cell carcinoma

What is Goblet cell carcinoma?

Goblet cell carcinoma (also called goblet cell adenocarcinoma, or previously goblet cell carcinoid) is a rare type of cancer that most commonly arises in the appendix. It gets its name from the goblet-shaped cells that are normally found lining the intestines and produce mucus. This cancer is unique because it has features of both a carcinoid (neuroendocrine) tumor and a traditional adenocarcinoma, making it a mixed or hybrid tumor type. It tends to behave more aggressively than typical carcinoid tumors of the appendix. Patients with goblet cell carcinoma may initially have no symptoms at all

How is Goblet cell carcinoma inherited?

Goblet cell carcinoma follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Goblet cell carcinoma typically begin?

Typical onset of Goblet cell carcinoma is adult. Age of onset can vary across affected individuals.

Which specialists treat Goblet cell carcinoma?

3 specialists and care centers treating Goblet cell carcinoma are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.