Treatments for Glycogen storage disease due to acid maltase deficiency

FDA-approved drugs, patient assistance programs, and travel grants tracked on UniteRare for this condition.

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Treatment data is extracted from FDA drug labels, DailyMed, and openFDA through automated and AI-assisted pipelines that read both structured records and unstructured label text.

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FDA-approved treatments (4)

Omeprazole
OMEPRAZOLE
PD-Rx Pharmaceuticals, Inc.
Pombiliti and Opfolda
cipaglucosidase alfa-atga and miglustat
Amicus Therapeutics, Inc.
Approved Sep 2023
Nexviazyme
AVALGLUCOSIDASE ALFA-NGPT
Genzyme Corporation
Approved Aug 2021
Myozyme
Recombinant human acid alpha-glucosidase; alglucosidase alfa
Genzyme Corporation
Approved Apr 2006

Patient support programs (2)

Copay cards, manufacturer assistance, and foundation grants. Verification status shown on each card.

Pombiliti and Opfolda

Amicus Therapeutics, Inc.

Verified 6d ago

copay card

copay assistancePatient Assistance

Accepting applications

Copay Card Apply

Myozyme

Genzyme Corporation

Unverified — confirm before calling

copay card

copay assistancePatient Assistance

Accepting applications

FDA-approved treatments (4)

Patient support programs (2)

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