Specialists for Glycogen storage disease due to acid maltase deficiency
29 physicians and care centers identified from ClinicalTrials.gov trial PIs, PubMed publications, and the NPPES NPI registry.
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Specialists are identified from ClinicalTrials.gov principal investigators, PubMed publications, and the NPI registry, then ranked through an automated scoring pipeline.
Report missing data- Yin-Hsiu Chien, MD, PhDRare Disease / Clinical ResearchNational Taiwan University HospitalQC-verified PI×2
- Tahseen Mozaffar, MD, MDRare Disease / Clinical ResearchUniversity of California Irvine HealthORANGE, CAPI×3
- Ozlem Goker-Alpan, MDRare Disease SpecialistLysosomal & Rare Disorders Research & Treatment Center, Inc.Fairfax, VirginiaPI×9
- Whu-Liang Hwu, MD, PhDRare Disease / Clinical ResearchNational Taiwan University HospitalPI×3
- Joseph Rossano, MD, M.DRare Disease / Clinical ResearchChildren's Hospital of PhiladelphiaPHILADELPHIA, PAPI×2
- Filip K Knop, MD, PhDRare Disease / Clinical ResearchUniversity Hospital, Gentofte, CopenhagenPI×5
- Use Central ContactRare Disease / Clinical ResearchAstellas Pharma IncPI×31
- Harrison Jones, PhDRare Disease / Clinical ResearchDuke UniversityPI×5
- Barry J Byrne, MD, PhD, MDRare Disease / Clinical ResearchUniversity of FloridaGAINESVILLE, FLPI×3
- Lea Bentur, Prof.Rare Disease / Clinical ResearchRambam MCPI×5
- Manuela Corti, PT, PhDRare Disease / Clinical ResearchUniversity of FloridaPI×2
- Hal Landy, MD, M.DRare Disease / Clinical ResearchValerion Therapeutics, LLCDOVER, MAPI×5
- Stephan Wenninger, PD Dr. med.Rare Disease / Clinical ResearchNeurologistPI×2
- Barbara K Smith, PT, PhDRare Disease / Clinical ResearchUniversity of FloridaPI×3
- Karen L Madsen, MD, MDRare Disease / Clinical ResearchNeuromuscular Research Unit, RigshospitaletMILWAUKEE, WIPI×3
- Boehringer IngelheimRare Disease SpecialistThe Institute for Liver Health II DBA Arizona Clinical TrialsPeoria, ArizonaPI×157
- Jordi Díaz ManeraFundació Institut de Recerca de l'Hospital de la Santa Creu i Sant PauQC-verified PI×1
- Paolo BanfiIRCCS Fondazione Don Carlo GnocchiQC-verified PI×1
- Pieter A. van DoornErasmus Medical CenterQC-verified PI×1
- Dwight KoeberlDuke UniversityDURHAM, NCQC-verified PI×2
- Dwight D KoeberlDuke UniversityDURHAM, NCQC-verified PI×3
- Guang YangChinese PLA General HospitalQC-verified PI×1
- Serhat GumrukcuSeraph Research InstituteQC-verified PI×1
- Helge AmthorHôpital Raymond PoincaréQC-verified PI×1
- Michael PrzybylskiCentre for Analytical Biochemistry, 65428 Ruesselsheim am Main, GermanyQC-verified PI×1
- Regina TrollmannUniversity Hospital ErlangenQC-verified PI×1
- Mark TarnopololskyMcMaster UniversityQC-verified PI×1
- Alfred E SlonimColumbia UniversityQC-verified PI×1
- Irina Kline, LCSWAmicus TherapeuticsWYOMISSING, PAQC-verified PI×1