Gestational trophoblastic neoplasm

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1Active trials19Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Gestational trophoblastic neoplasm (GTN) is a group of rare tumors that grow from cells that normally form the placenta during pregnancy. These tumors can develop after any type of pregnancy — including a normal pregnancy, a miscarriage, or a molar pregnancy (also called a hydatidiform mole, where abnormal tissue grows in the uterus instead of a normal baby). GTN includes several types: invasive mole, choriocarcinoma, placental site trophoblastic tumor (PSTT), and epithelioid trophoblastic tumor (ETT). These tumors are sometimes grouped under the broader term gestational trophoblastic disease (GTD). GTN affects the uterus and can sometimes spread to other parts of the body, including the lungs, brain, and liver. Because these tumors produce a hormone called hCG (human chorionic gonadotropin — the same hormone detected in pregnancy tests), doctors can track the disease and treatment response through simple blood tests. Common symptoms include unusual vaginal bleeding after a pregnancy, a uterus that seems larger than expected, and pelvic pain. The good news is that GTN is one of the most treatable cancers known. Even when it has spread to other organs, most women are cured with chemotherapy. Fertility can often be preserved. Early detection and treatment at a specialist center lead to excellent outcomes for the vast majority of patients.

Also known as:

Key symptoms:

Unusual or heavy vaginal bleeding after a pregnancy, miscarriage, or molar pregnancyUterus larger than expected for the stage of pregnancyPelvic pain or pressureNausea and vomiting more severe than typical morning sicknessNo fetal heartbeat or fetal parts seen on ultrasound when expectedPersistently elevated pregnancy hormone (hCG) levels after a pregnancy endsShortness of breath or coughing (if tumor has spread to the lungs)Headache or neurological symptoms (if spread to the brain)Grape-like clusters of tissue passed from the vaginaSwollen or painful ovaries due to ovarian cysts

Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Adult

Begins in adulthood (age 18 or older)

Orphanet ↗NORD ↗

FDA & Trial Timeline

10 events
Nov 2026Enhancing Wound Perfusion in High-Risk Lower Extremity Orthopaedic Surgery: A Study on Nitropaste Using Intraoperative SPY Imaging.

Johns Hopkins University — PHASE1

TrialNOT YET RECRUITING
Apr 2026A Study to Learn About How Safe Nitroglycerin is and How it Affects the Body When Taken Along With Nurandociguat in People With Coronary Artery Disease

Bayer — PHASE1

TrialNOT YET RECRUITING
Feb 2026Comparing of Sesame Oil, Nitroglycerin Ointment, and Aloe Vera Gel

University of Basrah — PHASE2

TrialNOT YET RECRUITING
Feb 2026Nitroglycerin Ointment for Pain Relief After Endoscopic Hemorrhoid Band Ligation

Ying Zhu — PHASE4

TrialNOT YET RECRUITING
Oct 2025NICardipine for Fast Achievement of Systolic BP Targets in ICH

Aarhus University Hospital — PHASE4

TrialNOT YET RECRUITING
Sep 2025Precise Endoscopic Application of Nitroglycerin in Preventing Post-ERCP Pancreatitis

National Cheng-Kung University Hospital — PHASE4

TrialRECRUITING
Aug 2025"Lignocaine vs GTN Ointment for Postoperative Pain After Hemorrhoidectomy")

King Edward Medical University — NA

TrialRECRUITING
Jul 2025A Multi-center Cohort Study of Hydatidiform Mole in China (CN-HM-01)

Obstetrics & Gynecology Hospital of Fudan University

TrialRECRUITING
May 2025Analysis of Coronary Reactivity Testing With and Without Intracoronary Nitrate Testing

Baylor Research Institute — NA

TrialRECRUITING
Apr 2025The FOCUS-ADHF Registry

ASL Città di Torino

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Gestational trophoblastic neoplasm.

1 clinical trialare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

1 recruitingView all trials with filters →
Other1 trial
A Multi-center Cohort Study of Hydatidiform Mole in China (CN-HM-01)
Actively Recruiting
PI: Xin Lu, MD & PhD (Obstetrics & Gynecology Hospital of Fudan Universi) · Sites: Lanzhou, Gansu; Shenzhen, Guangdong +12 more · Age: 1860 yrs

Specialists

19 foundView all specialists →
XX
Xing Xie
Specialist
PI on 1 active trial177 Gestational trophoblastic neoplasm publications
SP
Sandip P Patel
Birmingham, Alabama
Specialist

Rare Disease Specialist

PI on 1 active trial
PM
Paul Martin
Specialist
PI on 3 active trials73 Gestational trophoblastic neoplasm publications
JS
Julian C Schink
CHICAGO, IL
Specialist
PI on 1 active trial
IP
Ira Winer, MD PhD
DETROIT, MI
Specialist
PI on 1 active trial
DK
David Kushner
Specialist
PI on 2 active trials4 Gestational trophoblastic neoplasm publications
JP
Joseph Bubalo, PharmD
PORTLAND, OR
Specialist
PI on 2 active trials
SM
Sameh Emile, M.D.
Specialist
PI on 4 active trials
KS
Kamaljit Singh
Specialist
PI on 1 active trial129 Gestational trophoblastic neoplasm publications
MM
Mrinalini Balki, MD
Specialist
PI on 2 active trials
JH
Jakob Møller Hansen
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Gestational trophoblastic neoplasm.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Gestational trophoblastic neoplasm

Disease timeline:

New recruiting trial: Analysis of Coronary Reactivity Testing With and Without Intracoronary Nitrate Testing

A new clinical trial is recruiting patients for Gestational trophoblastic neoplasm

New recruiting trial: Postprocedural Contrast Mediated FFR Plus Intracoronary Infusion of Nitroglycerin in Multivessel Patients (PROMETEUS TRIAL)

A new clinical trial is recruiting patients for Gestational trophoblastic neoplasm

New recruiting trial: The FOCUS-ADHF Registry

A new clinical trial is recruiting patients for Gestational trophoblastic neoplasm

New recruiting trial: "The Effect of Inhaled Nitroglycerin for COPD Patients

A new clinical trial is recruiting patients for Gestational trophoblastic neoplasm

New recruiting trial: Aerobic Exercise-induced Effect on Endothelial Function in Patients With Ischaemic Heart Disease

A new clinical trial is recruiting patients for Gestational trophoblastic neoplasm

New recruiting trial: Precise Endoscopic Application of Nitroglycerin in Preventing Post-ERCP Pancreatitis

A new clinical trial is recruiting patients for Gestational trophoblastic neoplasm

New recruiting trial: "Lignocaine vs GTN Ointment for Postoperative Pain After Hemorrhoidectomy")

A new clinical trial is recruiting patients for Gestational trophoblastic neoplasm

New recruiting trial: Nitroglycerin Plus Radiotherapy Versus Conventional Radiotherapy in Patients With Lung Cancer.

A new clinical trial is recruiting patients for Gestational trophoblastic neoplasm

New recruiting trial: Avelumab and Methotrexate in in Low-risk Gestational Trophoblastic Neoplasias as First Line Treatment

A new clinical trial is recruiting patients for Gestational trophoblastic neoplasm

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What type of GTN do I have, and what does that mean for my treatment and prognosis?,Will I still be able to get pregnant after treatment?,How long will I need to be monitored after treatment ends, and what does follow-up involve?,Should I be treated at a specialized trophoblastic disease center?,What are the side effects of the chemotherapy you are recommending, and how can they be managed?,What are the signs that the disease has come back, and what should I do if I notice them?,Are there any clinical trials I should consider if standard treatment does not work?

Common questions about Gestational trophoblastic neoplasm

What is Gestational trophoblastic neoplasm?

Gestational trophoblastic neoplasm (GTN) is a group of rare tumors that grow from cells that normally form the placenta during pregnancy. These tumors can develop after any type of pregnancy — including a normal pregnancy, a miscarriage, or a molar pregnancy (also called a hydatidiform mole, where abnormal tissue grows in the uterus instead of a normal baby). GTN includes several types: invasive mole, choriocarcinoma, placental site trophoblastic tumor (PSTT), and epithelioid trophoblastic tumor (ETT). These tumors are sometimes grouped under the broader term gestational trophoblastic disease

How is Gestational trophoblastic neoplasm inherited?

Gestational trophoblastic neoplasm follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Gestational trophoblastic neoplasm typically begin?

Typical onset of Gestational trophoblastic neoplasm is adult. Age of onset can vary across affected individuals.

Are there clinical trials for Gestational trophoblastic neoplasm?

Yes — 1 recruiting clinical trial is currently listed for Gestational trophoblastic neoplasm on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Gestational trophoblastic neoplasm?

19 specialists and care centers treating Gestational trophoblastic neoplasm are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.