Familial Hypophosphatemia

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What is Familial Hypophosphatemia?

Familial Hypophosphatemia is treated with 14 medications in our database, including SEVELAMER CARBONATE, Ergocalciferol, CRYSVITA, POTASSIUM PHOSPHATES, Sevelamer carbonate, and 9 more. 8 of these have manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Sanofi, Validus Pharmaceuticals, Ultragenyx, Fresenius Kabi, Alexion and others. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Familial Hypophosphatemia treatment below.

Inheritance
Variable
Can be inherited in different ways depending on the underlying gene
Age of Onset
Childhood
Begins in childhood, roughly ages 1 to 12
NORD ↗

Treatments

0 FDA-approved · 10 other tracked

Source: openFDA + DailyMed · NDA / BLA labels with structured indications · refreshed weekly

Other tracked therapies (10)

Medications tracked in our therapeutics database that are not FDA-approved for Familial Hypophosphatemia via a labelled indication. May include investigational, off-label, or supportive therapies. Always verify with a clinician before use.

Potassium Phosphate

Leucine, Phenylalanine, Lysine, Methionine, Isoleucine, Valine, Histidine, Threonine, Tryptophan, Alanine, Glycine, Arginine, Proline, Serine, Tyrosine, Sodium Acetate, Dibasic Potassium Phosphate, Ma· UnknownNot FDA-labelled for Familial Hypophosphatemia

Detailed copay and financial assistance information is not publicly available for this medication at this time. Please consult your pharmacist or the manufacturer's official patient support program fo

POTASSIUM PHOSPHATES

Potassium Phosphate, Monobasic Potassium Phosphate, Dibasic· Fresenius KabiNot FDA-labelled for Familial Hypophosphatemia

Detailed copay and financial assistance information is not publicly available for this medication at this time. Please consult your pharmacist or the manufacturer's official patient support program fo

ERGOCALCIFEROL

ergocalciferol· SanofiNot FDA-labelled for Familial Hypophosphatemia

Detailed copay and financial assistance information is not publicly available for this medication at this time. Please consult your pharmacist or the manufacturer's official patient support program fo

VITAMIN D

ergocalciferol· SanofiNot FDA-labelled for Familial Hypophosphatemia

Detailed copay and financial assistance information is not publicly available for this medication at this time. Please consult your pharmacist or the manufacturer's official patient support program fo

Sodium Phosphates

sodium phosphate, monobasic, monohydrate and sodium phosphate, dibasic, anhydrous· C.B. Fleet Company, Inc.Not FDA-labelled for Familial Hypophosphatemia

Detailed copay and financial assistance information is not publicly available for this medication at this time. Please consult your pharmacist or the manufacturer's official patient support program fo

Ferric Citrate

Ferric Citrate· AkebiaNot FDA-labelled for Familial Hypophosphatemia

• Patient Copay Amount: Not Publicly Available • Maximum Annual Benefit Limit: Not Publicly Available • Core Eligibility Restrictions: Not Publicly Available • RxBIN, PCN, and Group numbers: Not Publi

Sevelamer Carbonate

SEVELAMER CARBONATE· DR. REDDY'S LABORATORIES LIMITEDNot FDA-labelled for Familial Hypophosphatemia

* Patient Copay Amount: Not Publicly Available * Maximum Annual Benefit Limit: Not Publicly Available * Core Eligibility Restrictions: U.S. Residents Only * RxBIN, PCN, and Group numbers: Not Publicly

STRENSIQ

ASFOTASE ALFA· AlexionNot FDA-labelled for Familial Hypophosphatemia

* Patient Copay Amount: Not Publicly Available * Maximum Annual Benefit Limit: Not Publicly Available * Core Eligibility Restrictions: Not Publicly Available * RxBIN, PCN, and Group numbers: Not Publi

Ergocalciferol Capsules,

ergocalciferol· SanofiNot FDA-labelled for Familial Hypophosphatemia

Detailed copay and financial assistance information is not publicly available for this medication at this time. Please consult your pharmacist or the manufacturer's official patient support program fo

CRYSVITA

Burosumab· UltragenyxNot FDA-labelled for Familial Hypophosphatemia

* Patient Copay Amount: Not Publicly Available * Maximum Annual Benefit Limit: Not Publicly Available (The program covers costs up to a specified maximum benefit per calendar year, but the specific d

Source: ClinicalTrials.gov · synced daily · phases, status, and PI names normalized at ingest

No actively recruiting trials found for Familial Hypophosphatemia at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Familial Hypophosphatemia community →

Specialists

1 foundView all specialists →

Source: NPI Registry + PubMed · trial PI roles cross-referenced with ClinicalTrials.gov · ranked by match score (publications + PI activity + community signal)

CB
Clemens Bergwitz, MD
NEW HAVEN, CT
Specialist

Endocrinology

Yale University

Last updated · May 2026PI on 1 active trial

Treatment Centers

8 centers

Source: NORD Rare Disease Centers + NIH Undiagnosed Diseases Network (UDN) · centers verified active within last 12 months

🏨 Children's

Children's Hospital Colorado Rare Disease Program

Children's Hospital Colorado

📍 Aurora, CO

👤 Boston Children's Hospital Rare Disease Program

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Boston Children's Hospital Rare Disease Program

Boston Children's Hospital

📍 Boston, MA

👤 Boston Children's Hospital Rare Disease Program

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

🏨 Children's

Ann & Robert H. Lurie Children's Hospital Genetics

Lurie Children's Hospital

📍 Chicago, IL

👤 Boston Children's Hospital Rare Disease Program

🏥 NORD

Cincinnati Children's Hospital Medical Center

Cincinnati Children's

📍 Cincinnati, OH

👤 Boston Children's Hospital Rare Disease Program

🏨 Children's

Nationwide Children's Hospital Rare Disease Center

Nationwide Children's Hospital

📍 Columbus, OH

👤 Boston Children's Hospital Rare Disease Program

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

Travel Grants

No travel grants are currently matched to Familial Hypophosphatemia.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Familial HypophosphatemiaForum →

No community posts yet. Be the first to share your experience with Familial Hypophosphatemia.

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Latest news about Familial Hypophosphatemia

Source: PubMed + NIH RePORTER + openFDA + clinical-journal RSS · last 30 days · disease-tagged at ingest by AI extraction with human QC

No recent news articles for Familial Hypophosphatemia.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Familial Hypophosphatemia

What is Familial Hypophosphatemia?

Familial Hypophosphatemia is treated with 14 medications in our database, including SEVELAMER CARBONATE, Ergocalciferol, CRYSVITA, POTASSIUM PHOSPHATES, Sevelamer carbonate, and 9 more. 8 of these have manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Sanofi, Validus Pharmaceuticals, Ultragenyx, Fresenius Kabi, Alexion and others. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Familial Hypophosphatemia treatment below.

At what age does Familial Hypophosphatemia typically begin?

Typical onset of Familial Hypophosphatemia is childhood. Age of onset can vary across affected individuals.

Which specialists treat Familial Hypophosphatemia?

1 specialists and care centers treating Familial Hypophosphatemia are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.

What treatment and support options exist for Familial Hypophosphatemia?

10 FDA-approved treatments are currently tracked on UniteRare for Familial Hypophosphatemia. See the treatments and support programs sections for copay assistance, eligibility, and contact details.

Frequently asked questions about Familial Hypophosphatemia

Auto-generated from canonical disease facts (Orphanet, OMIM, ClinicalTrials.gov, openFDA, NPPES). Not a substitute for clinical guidance.

  1. What is Familial Hypophosphatemia?

    Familial Hypophosphatemia is a rare disease catalogued in international rare-disease ontologies. It is typically inherited as variable. Age of onset is generally childhood. For verified primary sources, see the UniteRare Familial Hypophosphatemia page.

  2. How is Familial Hypophosphatemia inherited?

    Familial Hypophosphatemia follows variable inheritance. Genetic counseling is recommended for affected families to understand recurrence risk in offspring and the likelihood of unaffected siblings being carriers. Variants in the underlying gene(s) may be identified via clinical genetic testing.

  3. Are there FDA-approved treatments for Familial Hypophosphatemia?

    Yes — UniteRare tracks 10 FDA-approved treatments with indications relevant to Familial Hypophosphatemia. Each entry includes prescribing information, orphan-drug-designation status where applicable, and the FDA application number for verification.

  4. Are there clinical trials for Familial Hypophosphatemia?

    Active clinical trials for Familial Hypophosphatemia are tracked daily from ClinicalTrials.gov. Trial availability changes frequently; check the UniteRare trial listings for the current count and recruitment status. Sponsors of rare-disease research often welcome inquiries even when a trial is not actively recruiting at a given moment.

  5. How do I find a specialist for Familial Hypophosphatemia?

    UniteRare lists 1 verified clinician with documented expertise in Familial Hypophosphatemia, sourced from ClinicalTrials.gov principal-investigator records, PubMed publication histories, and the NPPES NPI registry. Filter by state or browse our state-specific specialist pages for nearby options.

See full Familial Hypophosphatemia page for complete clinical details, sources, and verified-specialist listings.

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