Dysraphism-cleft lip/palate-limb reduction defects syndrome

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Overview

Dysraphism-cleft lip/palate-limb reduction defects syndrome is an extremely rare condition present from birth that affects several parts of the body at the same time. 'Dysraphism' refers to problems with the neural tube — the structure that forms the brain and spinal cord during early pregnancy. When this does not close properly, it can lead to serious defects of the spine and brain. Children with this syndrome also tend to be born with a cleft lip and/or cleft palate, which means there is a gap or split in the upper lip or the roof of the mouth. In addition, they may have limb reduction defects, meaning that one or more limbs (arms or legs) may be underdeveloped, shorter than normal, or partially missing. This combination of features makes the syndrome very complex and affects multiple body systems from birth. The exact cause is not fully understood, and only a very small number of cases have been reported in the medical literature. Because of this, doctors and researchers still have much to learn about why it happens and how best to treat it. Treatment focuses on managing each individual problem rather than curing the underlying condition. Surgical repair of the cleft lip and palate is usually done in infancy. Spinal defects may require surgery and ongoing neurological care. Limb differences are managed with prosthetics, physical therapy, and occupational therapy. A team of specialists working together gives children the best chance at a good quality of life.

Also known as:

Key symptoms:

Incomplete closure of the spine or brain (neural tube defect)Cleft lip — a split or gap in the upper lipCleft palate — an opening in the roof of the mouthMissing or underdeveloped arms or legs (limb reduction defects)Possible paralysis or weakness in the legs depending on spinal involvementBladder and bowel control problems related to spinal defectsDifficulty feeding in infancy due to cleft palatePossible hydrocephalus (fluid buildup in the brain)Increased risk of infections such as meningitis if the spinal cord is exposedPossible intellectual or developmental delays depending on brain involvement

Clinical phenotype terms (9)— hover any for plain English
GastroschisisHP:0001543AnencephalyHP:0002323Ectopic anusHP:0004397
Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Dysraphism-cleft lip/palate-limb reduction defects syndrome.

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No actively recruiting trials found for Dysraphism-cleft lip/palate-limb reduction defects syndrome at this time.

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No specialists are currently listed for Dysraphism-cleft lip/palate-limb reduction defects syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Dysraphism-cleft lip/palate-limb reduction defects syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Dysraphism-cleft lip/palate-limb reduction defects syndrome

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

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Social Security Disability

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Questions for your doctor

Bring these to your next appointment

  • Q1.What is the full extent of my child's spinal defect, and what does that mean for their movement and bladder control?,What surgeries will my child need, and in what order should they happen?,Should we do genetic testing, and what might it tell us about the cause and risk for future pregnancies?,What therapies should we start right away, and how often will my child need them?,Are there any specialists or centers with experience in this specific combination of conditions?,What signs should prompt me to seek emergency care?,What support services or patient organizations are available to help our family?

Common questions about Dysraphism-cleft lip/palate-limb reduction defects syndrome

What is Dysraphism-cleft lip/palate-limb reduction defects syndrome?

Dysraphism-cleft lip/palate-limb reduction defects syndrome is an extremely rare condition present from birth that affects several parts of the body at the same time. 'Dysraphism' refers to problems with the neural tube — the structure that forms the brain and spinal cord during early pregnancy. When this does not close properly, it can lead to serious defects of the spine and brain. Children with this syndrome also tend to be born with a cleft lip and/or cleft palate, which means there is a gap or split in the upper lip or the roof of the mouth. In addition, they may have limb reduction defec

At what age does Dysraphism-cleft lip/palate-limb reduction defects syndrome typically begin?

Typical onset of Dysraphism-cleft lip/palate-limb reduction defects syndrome is neonatal. Age of onset can vary across affected individuals.