Congenital high-molecular-weight kininogen deficiency

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:483OMIM:228960D68.8
Who is this for?
Show terms as
8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Congenital high-molecular-weight kininogen deficiency, also known as Fitzgerald factor deficiency, Williams trait, or Flaujeac trait, is a very rare inherited blood disorder. It affects a protein in the blood called high-molecular-weight kininogen (HMWK or HK), which plays a role in the contact activation pathway — a part of the blood clotting system. When this protein is missing or not working properly, certain laboratory clotting tests come back abnormal, which can be alarming at first. Despite the abnormal lab results, most people with this condition do not actually experience unusual bleeding in everyday life. This is one of the most important things to understand: the deficiency shows up strongly in a test called the aPTT (activated partial thromboplastin time), making it look like there is a serious clotting problem, but in reality the body usually clots normally during surgery, injury, or childbirth. This is because HMWK is not essential for the body's main clotting response in real-life situations. Because this condition is so rare and causes no real bleeding symptoms, it is most often discovered by accident — for example, when routine pre-surgical blood tests come back abnormal. Treatment is generally not needed. The main challenge is making sure doctors recognize this harmless condition so that patients are not given unnecessary treatments or denied needed procedures out of concern for bleeding risk.

Key symptoms:

No bleeding symptoms in most casesAbnormal result on a routine blood clotting test (aPTT) found by accidentPossible mild issues with blood vessel function in very rare casesNo increased risk of bruising in daily lifeNo increased bleeding during surgery or childbirth in most reported cases

Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Congenital high-molecular-weight kininogen deficiency.

View clinical trials →

No actively recruiting trials found for Congenital high-molecular-weight kininogen deficiency at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Congenital high-molecular-weight kininogen deficiency community →

No specialists are currently listed for Congenital high-molecular-weight kininogen deficiency.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Congenital high-molecular-weight kininogen deficiency.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Congenital high-molecular-weight kininogen deficiencyForum →

No community posts yet. Be the first to share your experience with Congenital high-molecular-weight kininogen deficiency.

Start the conversation →

Latest news about Congenital high-molecular-weight kininogen deficiency

No recent news articles for Congenital high-molecular-weight kininogen deficiency.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Does my abnormal clotting test mean I am at risk for serious bleeding during surgery or injury?,Do I need any treatment, or is it safe to leave this condition untreated?,Should my family members be tested for this condition?,What should I tell surgeons or dentists before a procedure?,Should I carry any medical documentation or alert card about my diagnosis?,Are there any activities or medications I should avoid?,Is there a specialist or center with experience in rare clotting disorders I should see?

Common questions about Congenital high-molecular-weight kininogen deficiency

What is Congenital high-molecular-weight kininogen deficiency?

Congenital high-molecular-weight kininogen deficiency, also known as Fitzgerald factor deficiency, Williams trait, or Flaujeac trait, is a very rare inherited blood disorder. It affects a protein in the blood called high-molecular-weight kininogen (HMWK or HK), which plays a role in the contact activation pathway — a part of the blood clotting system. When this protein is missing or not working properly, certain laboratory clotting tests come back abnormal, which can be alarming at first. Despite the abnormal lab results, most people with this condition do not actually experience unusual blee

How is Congenital high-molecular-weight kininogen deficiency inherited?

Congenital high-molecular-weight kininogen deficiency follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.