Specialists for Autosomal dominant adult-onset proximal spinal muscular atrophy
33 physicians and care centers identified from ClinicalTrials.gov trial PIs, PubMed publications, and the NPPES NPI registry.
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Specialists are identified from ClinicalTrials.gov principal investigators, PubMed publications, and the NPI registry, then ranked through an automated scoring pipeline.
Report missing data- Eugenio Mercuri, MDRare Disease SpecialistIstituto GasliniGenovaPI×3
- Laurent Servais, MDRare Disease / Clinical ResearchCentre Hospitalier Universitaire de LiegePI×6 1
- Richard S Bedlack, MD, PhD, M.D. Ph.DRare Disease / Clinical ResearchDuke UniversityDURHAM, NCPI×2
- Kenneth H Fischbeck, M.D., M.DRare Disease / Clinical ResearchNational Institute of Neurological Disorders and Stroke (NINDS)BETHESDA, MDPI×6
- May Orfali, MDRare Disease / Clinical ResearchGemma BiotherapeuticsPI×3
- Jacqueline Montes, Pt, EdDRare Disease SpecialistColumbia UniversityNew York, New YorkPI×5
- Otávio Berwanger, PhDRare Disease SpecialistHospital Albert EinsteinBuenos Aires, Buenos Aires F.D.PI×3
- Susana QUIJANO-ROY, MD, PhDRare Disease / Clinical ResearchRaymond Poincaré Hospital, Garches, FRANCEPI×3
- Matthew ER Butchbach, Ph.D.Rare Disease / Clinical ResearchNemours Children's ClinicPI×2
- Melodi Pirzada, MD, MDRare Disease / Clinical ResearchSt Mary's Healthcare System for ChildrenMINEOLA, NYPI×4
- Enrico Bertini, MDRare Disease / Clinical ResearchBambino Gesù Children's Hospital, Department of NeurosciencesPI×4
- Dr Ching H. WangRare Disease / Clinical ResearchStanford UniversityPI×2 528
- Matthew Harms, MD, M.DRare Disease / Clinical ResearchColumbia UniversityLAWRENCE, KSPI×2
- Walter Truong, MD, M.DRare Disease / Clinical ResearchGillette Children's Specialty HealthcareST. PAUL, MNPI×2 1
- Emmanuel ROZE, MDRare Disease / Clinical ResearchInstitut National de la Santé Et de la Recherche Médicale, FrancePI×2
- Marco CapogrossoRare Disease / Clinical ResearchUniversity of PittsburghPI×2
- Minal J Bhanushali, MDNational Institute of Neurological Disorders and Stroke (NINDS)PALO ALTO, CAQC-verified PI×1
- Charlotte LilienUniversity of Oxford, Department of PaediatricsQC-verified PI×1
- Yi-Ning suNational Taiwan University HospitalQC-verified PI×2
- Chayada TangshewinsirikulRamathibodi Hospital, Mahidol UniversityQC-verified PI×1
- John T Kissel, PTOhio State UniversityCHURCHVILLE, NYQC-verified PI×1
- Liang-Wey ChangRehabilitation Engineering Lab,NTUQC-verified PI×1
- Samra Hamzic, MAUniversity GiessenQC-verified PI×1
- Bruno A ZanfiniFondazione Policlinico A. GemelliQC-verified PI×1
- Andriy V. ShatilloState Institution "Institute of Neurology, Psychiatry and Narcology of NAMS of Ukraine"QC-verified PI×1
- Bakri Elsheikh, MDOhio State UniversityCOLUMBUS, OHQC-verified PI×3
- Yuh Jyh JongVice President, Kaohsiung Medical UniversityQC-verified PI×1
- Maria A. Jones, PTUniversity of OklahomaQC-verified PI×1
- Brigitte Estournet, Pu-phAssistance Publique - Hôpitaux de ParisQC-verified PI×1
- AveXis MedinfoSponsor GmbHQC-verified PI×1
- Naime Evrim Karadag SaygiDepartment of PM&R, Marmara University School of MedicineQC-verified PI×1
- Erik Hulzebos, DrUMC UtrechtQC-verified PI×1
- Uwe MelliesUniversity of Essen, GermanyQC-verified PI×1