Acquired generalized lipodystrophy

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1FDA treatments6Active trials30Specialists8Treatment centers1Financial resources

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Overview

Acquired generalized lipodystrophy (AGL), also known as Lawrence syndrome or Lawrence-Seip syndrome, is a rare condition where the body loses most of its fat tissue (adipose tissue) under the skin and around the organs. Unlike inherited forms of lipodystrophy, AGL develops during a person's lifetime — it is not present at birth. The fat loss usually happens gradually and affects the whole body, giving the skin a thin, almost muscular appearance. Because fat tissue plays an important role in storing energy and producing hormones like leptin, losing it causes serious problems throughout the body. People with AGL often develop insulin resistance, which means the body cannot use blood sugar properly, leading to diabetes. High levels of fats (triglycerides) in the blood are also very common and can cause dangerous inflammation of the pancreas. The liver often becomes enlarged and filled with fat, which can lead to liver disease over time. Treatment focuses on managing complications rather than curing the condition. A strict low-fat, low-sugar diet is a cornerstone of care. Metreleptin (brand name Myalept), a synthetic form of the hormone leptin, is FDA-approved and has significantly improved outcomes for many patients by helping control blood sugar and triglyceride levels. Regular monitoring by a team of specialists is essential to prevent serious long-term complications.

Also known as:

Key symptoms:

Loss of fat tissue under the skin across the whole bodyVisible muscles and veins due to lack of body fatHigh blood sugar or diabetesVery high triglyceride (blood fat) levelsEnlarged liver (hepatomegaly)Fatty liver diseaseAcanthosis nigricans — dark, velvety patches of skin, often in skin foldsEnlarged spleenIrregular or absent menstrual periods in womenExcessive hunger and appetiteFatigue and low energyAbdominal pain (sometimes from pancreatitis)Polycystic ovary syndrome (PCOS)-like symptoms in women

Clinical phenotype terms (28)— hover any for plain English
Generalized lipodystrophyHP:0009064Abnormal circulating lipid concentrationHP:0003119Calf muscle pseudohypertrophyHP:0003707Progeroid facial appearanceHP:0005328Abnormal cardiovascular system physiologyHP:0011025Acute pancreatitisHP:0001735
Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

FDA & Trial Timeline

10 events
Mar 2026Efficacy and Safety of Mibavademab in Adult and Pediatric Patients With Generalized Lipodystrophy

Regeneron Pharmaceuticals — PHASE3

TrialRECRUITING
May 2025Open-label Study to Evaluate Metreleptin in Children Under 6 Years of Age With Generalised Lipodystrophy

Amryt Pharma — PHASE3

TrialRECRUITING
Apr 2025Granzyme B-targeted PET Imaging Monitoring Tumor Responses to Immunotherapy

Zhongnan Hospital

TrialNOT YET RECRUITING
Mar 2025The Value of PET Imaging Targeting Granzyme B in Predicting Efficacy and Prognosis in T-NK Cell Lymphoma

Ruijin Hospital

TrialNOT YET RECRUITING
Dec 2024A Study of the Safety of Mibavademab in Pediatric and Adult Participants Switching From Metreleptin to Mibavademab for the Treatment of Generalized Lipodystrophy (GLD)

Regeneron Pharmaceuticals — PHASE3

TrialACTIVE NOT RECRUITING
Nov 2024GzmB-PET/CT to Evaluate Neoadjuvant Therapy Efficacy in Breast Cancer

Shanghai Jiao Tong University School of Medicine

TrialRECRUITING
May 202364Cu-GRIP B in Patients With Advanced Malignancies

Rahul Aggarwal — PHASE1, PHASE2

TrialRECRUITING
Aug 2020Pulmonary Hypertension Biorepository and Registry

University of Kansas Medical Center

TrialRECRUITING
Apr 2019Cyclophosphamide in the Treatment of Associated Acquired Lipodystrophy Syndrome With Type 1 Diabetes

Children's Hospital of Fudan University — NA

TrialACTIVE NOT RECRUITING
Dec 2017Registry for Patients With Lipodystrophy

University of Ulm

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

1 available

MYALEPT

metreleptin· Chiesi Farmaceutici S.p.A.■ Boxed Warning

indicated as an adjunct to diet as replacement therapy to treat the complications of leptin deficiency in patients with congenital or acquired generalized lipodystrophy

Clinical Trials

6 recruitingView all trials with filters →
Phase 34 trials
Efficacy and Safety of Mibavademab in Adult and Pediatric Patients With Generalized Lipodystrophy
Phase 3
Actively Recruiting
PI: Clinical Trial Management (Regeneron Pharmaceuticals) · Sites: Ann Arbor, Michigan · Age: 299 yrs
A Study of the Safety of Mibavademab in Pediatric and Adult Participants Switching From Metreleptin to Mibavademab for the Treatment of Generalized Lipodystrophy (GLD)
Phase 3
Active
PI: Clinical Trial Management (Regeneron Pharmaceuticals) · Sites: Bethesda, Maryland; Ann Arbor, Michigan · Age: 299 yrs
Open-label Study to Evaluate Metreleptin in Children Under 6 Years of Age With Generalised Lipodystrophy
Phase 3
Actively Recruiting
· Sites: Leuven; Paris +10 more · Age: 05 yrs
Compassionate Use of Metreleptin in Previously Treated People With Generalized Lipodystrophy
Phase 3
Active
PI: Rebecca J Brown, M.D. (National Institute of Diabetes and Digestive and K) · Sites: Bethesda, Maryland · Age: 098 yrs
N/A1 trial
Cyclophosphamide in the Treatment of Associated Acquired Lipodystrophy Syndrome With Type 1 Diabetes
N/A
Active
PI: Feihong Luo (Children's Hospital of Fudan University) · Sites: Shanghai, Shanghai Municipality
Other1 trial
Registry for Patients With Lipodystrophy
Actively Recruiting
PI: Martin Wabitsch, Prof. Dr. (University of Ulm) · Sites: Vienna; Lille +26 more

Specialists

Showing 25 of 30View all specialists →
CL
Christopher Liverman
ALBUQUERQUE, NM
Specialist
1 Acquired generalized lipodystrophy publication
FC
Fernando Corvillo
Specialist
1 Acquired generalized lipodystrophy publication
BA
Brent S Abel
IOWA CITY, IA
Specialist
1 Acquired generalized lipodystrophy publication
AL
Alberto López-Lera
Specialist
1 Acquired generalized lipodystrophy publication
GC
Giovanni Ceccarini
Specialist
1 Acquired generalized lipodystrophy publication
SM
Silvia Magno
Specialist
1 Acquired generalized lipodystrophy publication
FS
Ferruccio Santini
Specialist
1 Acquired generalized lipodystrophy publication
DA
David Araújo-Vilar
Specialist
1 Acquired generalized lipodystrophy publication
RB
Rebecca J Brown
Specialist
1 Acquired generalized lipodystrophy publication
PN
Pilar Nozal
Specialist
1 Acquired generalized lipodystrophy publication
ML
Margarita López-Trascasa
Specialist
1 Acquired generalized lipodystrophy publication
CM
Caleigh Mandel-Brehm
Specialist
1 Acquired generalized lipodystrophy publication
SV
Sara E Vazquez
Specialist
1 Acquired generalized lipodystrophy publication
MC
Mickie Cheng
SAN FRANCISCO, CA
Specialist
1 Acquired generalized lipodystrophy publication
AG
Abhimanyu Garg
DALLAS, TX
Specialist
2 Acquired generalized lipodystrophy publications
VM
Vanessa Rangel Miller, M.S., M.B.A
Specialist
PI on 1 active trial
LH
Lori Hartnett
OMAHA, NE
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Financial Resources

1 resources
MYALEPT(metreleptin)Chiesi Farmaceutici S.p.A.

Travel Grants

No travel grants are currently matched to Acquired generalized lipodystrophy.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Acquired generalized lipodystrophy

Disease timeline:

New recruiting trial: Pulmonary Hypertension Biorepository and Registry

A new clinical trial is recruiting patients for Acquired generalized lipodystrophy

New recruiting trial: 64Cu-GRIP B in Patients With Advanced Malignancies

A new clinical trial is recruiting patients for Acquired generalized lipodystrophy

New recruiting trial: Open-label Study to Evaluate Metreleptin in Children Under 6 Years of Age With Generalised Lipodystrophy

A new clinical trial is recruiting patients for Acquired generalized lipodystrophy

New recruiting trial: PET Imaging Targeting Granzyme B Predicts Immunotherapy Efficacy in Diffuse Large B-cell Lymphoma

A new clinical trial is recruiting patients for Acquired generalized lipodystrophy

New recruiting trial: GzmB-PET/CT to Evaluate Neoadjuvant Therapy Efficacy in Breast Cancer

A new clinical trial is recruiting patients for Acquired generalized lipodystrophy

New recruiting trial: Registry for Patients With Lipodystrophy

A new clinical trial is recruiting patients for Acquired generalized lipodystrophy

New recruiting trial: Efficacy and Safety of Mibavademab in Adult and Pediatric Patients With Generalized Lipodystrophy

A new clinical trial is recruiting patients for Acquired generalized lipodystrophy

New recruiting trial: MEASuRE: Metreleptin Effectiveness And Safety Registry

A new clinical trial is recruiting patients for Acquired generalized lipodystrophy

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What tests do I need to find out if there is an underlying cause for my fat loss, such as an autoimmune condition?,Am I a candidate for metreleptin (Myalept) therapy, and how do I access it?,What specific diet should I follow, and can I be referred to a specialist dietitian?,How often should I have my liver, blood sugar, and triglyceride levels checked?,What are the warning signs of pancreatitis or other emergencies I should watch for?,Are there any clinical trials or new treatments I should know about?,How will this condition affect my fertility or hormonal health long-term?

Common questions about Acquired generalized lipodystrophy

What is Acquired generalized lipodystrophy?

Acquired generalized lipodystrophy (AGL), also known as Lawrence syndrome or Lawrence-Seip syndrome, is a rare condition where the body loses most of its fat tissue (adipose tissue) under the skin and around the organs. Unlike inherited forms of lipodystrophy, AGL develops during a person's lifetime — it is not present at birth. The fat loss usually happens gradually and affects the whole body, giving the skin a thin, almost muscular appearance. Because fat tissue plays an important role in storing energy and producing hormones like leptin, losing it causes serious problems throughout the bod

How is Acquired generalized lipodystrophy inherited?

Acquired generalized lipodystrophy follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

Are there clinical trials for Acquired generalized lipodystrophy?

Yes — 6 recruiting clinical trials are currently listed for Acquired generalized lipodystrophy on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Acquired generalized lipodystrophy?

25 specialists and care centers treating Acquired generalized lipodystrophy are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.

What treatment and support options exist for Acquired generalized lipodystrophy?

1 patient support program are currently tracked on UniteRare for Acquired generalized lipodystrophy. See the treatments and support programs sections for copay assistance, eligibility, and contact details.