X-linked cerebral adrenoleukodystrophy

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At a Glance

Live from database

Regulatory Watchboard

No FDA or trial events recorded yet for X-linked cerebral adrenoleukodystrophy.

Financial Assistance

1 program

FINANCIAL LANDSCAPE SUMMARY

1

Total programs

1

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Patient Assistance Programs1

SKYSONA

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Approved Treatments

1 FDA-approved

Skysona

(ELIVALDOGENE AUTOTEMCEL)Orphan drugaccelerated

Genetix Biotherapeutics Inc.

12.1 Mechanism of Action SKYSONA adds functional copies of the ABCD1 cDNA into patients' hematopoietic stem cells (HSCs) through transduction of autol...

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Clinical Trial Landscape

No active clinical trials currently recruiting for X-linked cerebral adrenoleukodystrophy.
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Recent News & Research

No recent news articles indexed yet for X-linked cerebral adrenoleukodystrophy.
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Specialist Network

Top 6 by expertise

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