Showing 11 of 11 recruiting trials for “x-linked-cerebral-adrenoleukodystrophy”
Single Participant Study of an Experimental ASO Treatment for TUBB4A-related Leukodystrophy
A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel
A Clinical Study to Assess the Efficacy and Safety of Leriglitazone in Adult Male Subjects With Cerebral Adrenoleukodystrophy
An Open-Label Exploratory Study of Fosigotifator in Participants With Vanishing White Matter Disease
Home Exercise for Individuals with Neurodegenerative Disease
👨⚕️ Jennifer Keller, PT, Hugo W. Moser Research Institute at Kennedy Krieger, Inc.📍 1 site📅 Started Feb 2023View details ↗
RecruitingNCT03789721 ↗
Adrenoleukodystrophy National Registry Study
Precision Exercise in Children With Malignant Hemopathies
The Myelin Disorders Biorepository Project
👨⚕️ Adeline Vanderver, MD, Children's Hospital of Philadelphia📍 20 sites📅 Started Dec 2016View details ↗
UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
RecruitingNCT01668186 ↗
Longitudinal Natural History Study of Patients With Peroxisome Biogenesis Disorders (PBD)
👨⚕️ Nancy E Braverman, MD, MS, McGill University Health Center, Montreal Childrens Hopital📍 1 site📅 Started Jan 2012View details ↗
RecruitingNCT03639285 ↗
Natural History, Diagnosis, and Outcomes for Leukodystrophies
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