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FINANCIAL LANDSCAPE SUMMARY
Total programs
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Patient Assistance Programs1
CASGEVY
Vertex Pharmaceuticals Incorporated
CASGEVY
(EXAGAMGLOGENE AUTOTEMCEL)Orphan drugstandardVertex Pharmaceuticals Incorporated
FERRIPROX
(DEFERIPRONE)Orphan drugstandardChiesi USA, Inc.
Mitchell S Cairo, MD, MD
New York Medical College
📍 HAWTHORNE, NY
Abdullah Kutlar, MD, MD
Augusta University
📍 AUGUSTA, GA
Chen Jing, M.D.
Shanghai Children's Medical Center
📍 TORRANCE, CA
Haoquan Wu, PhD
R&D Kanglin Biotech
Juliano L Fernandes, MD
University of Campinas, Brazil
Himal Lal Thakar, MD, MD
bluebird bio, Inc.
📍 WATERBURY, CT