Beta-thalassemia major

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At a Glance

Live from database

Regulatory Watchboard

No FDA or trial events recorded yet for Beta-thalassemia major.

Financial Assistance

1 program

FINANCIAL LANDSCAPE SUMMARY

1

Total programs

1

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Patient Assistance Programs1

CASGEVY

Vertex Pharmaceuticals Incorporated

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Approved Treatments

2 FDA-approved

CASGEVY

(EXAGAMGLOGENE AUTOTEMCEL)Orphan drugstandard

Vertex Pharmaceuticals Incorporated

FDA label ↗

FERRIPROX

(DEFERIPRONE)Orphan drugstandard

Chiesi USA, Inc.

FDA label ↗

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Clinical Trial Landscape

No active clinical trials currently recruiting for Beta-thalassemia major.
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Recent News & Research

No recent news articles indexed yet for Beta-thalassemia major.
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Specialist Network

Top 6 by expertise

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