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Showing 20 of 32 recruiting trials for “beta-thalassemia-major

RecruitingNCT07215975

A Real-World Study to Evaluate Luspatercept in Adults With Transfusion-Dependent Beta-Thalassemia in the Middle East

👨‍⚕️ Bristol Myers Squibb, Bristol-Myers Squibb📍 2 sites📅 Started Feb 2026View details ↗
Enrolling by InvitationNCT07055503

Use of the Hemanext One® Hypoxic Red Blood Cell Storage System for Transfusion in Thalassemia Patients

👨‍⚕️ Antonis Kattamis, Professor, National and Kapodistrian University of Athens📍 1 site📅 Started Nov 2025View details ↗
NARecruitingNCT07207577

Evaluation of Physiological and Psychological Factors Involved in Exercise Intolerance in Patients With β-TTD

👨‍⚕️ Laurent MESSONNIER, Université Savoie Mont Blanc📍 1 site📅 Started Sep 2025View details ↗
Enrolling by InvitationNCT06717932

A Follow-up Study to Evaluate the Long-term Safety and Efficacy in Participants Who Received CS-101 Injection

🏥 CorrectSequence Therapeutics Co., Ltd📍 1 site📅 Started May 2025View details ↗
Phase 1, PHASE2RecruitingNCT06364774

ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia

👨‍⚕️ Janet Kwiatkowski, MD, Children's Hospital of Philadelphia📍 1 site📅 Started Apr 2025View details ↗
Enrolling by InvitationNCT06685536

A Long-term Follow-up Study in Participants Who Received CS-101

👨‍⚕️ Yongrong Lai, M.D., First Affiliated Hospital of Guangxi Medical University📍 1 site📅 Started Jan 2025View details ↗
Phase 1RecruitingNCT06772766

A Multiple Ascending Dose Study of 9MW3011 in Patients With Non-transfusion-dependent β-thalassemia

🏥 Mabwell (Shanghai) Bioscience Co., Ltd.📍 2 sites📅 Started Dec 2024View details ↗
NARecruitingNCT06734520

Clinical Study of Super Transplantation in the Treatment of Severe β-thalassemia

👨‍⚕️ Hua Jiang, PHD, Guangzhou Medical University Affiliated Women's and Children's Medical Center📍 2 sites📅 Started Oct 2024View details ↗
Phase 2RecruitingNCT06421636

A Study to Test the Safety, Tolerability, and Efficacy of an Antibody, REGN7999, Injected Under the Skin for the Treatment of Iron Overload in Adult Participants With Non-Transfusion Dependent β-thalassemia, Using MRI Scans to Measure Iron Levels in the Body

👨‍⚕️ Clinical Trial Management, Regeneron Pharmaceuticals📍 26 sites📅 Started Sep 2024View details ↗
Phase 4RecruitingNCT06606886

Effects of Hydroxyurea and Metformin in Transfusion Dependent Beta-Thalassemia

👨‍⚕️ Ayesha Khan, MBBS MPhil, Bahria University Islamabad📍 1 site📅 Started Sep 2024View details ↗
NARecruitingNCT06568926

Adherence of Beta Thalssemia Patients to Oral Chelation Therapy

🏥 Sohag University📍 1 site📅 Started Jul 2024View details ↗
NARecruitingNCT06479616

A Long-term Follow-up Study in Participants Who Received CS-101

👨‍⚕️ Xiaowen Zhai, M.D., Children's Hospital of Fudan University📍 1 site📅 Started Jun 2024View details ↗
NARecruitingNCT06466304

Inspiratory Muscle Training in Children With Beta Thalasemia

👨‍⚕️ hagar el-hadidy, lecturer, Faculty of Physical Therapy, Ahram Canadian University (ACU), Giza, Egypt📍 1 site📅 Started Jun 2024View details ↗
Phase 1, PHASE2RecruitingNCT06308159

An Open-label Study of a Gene Therapy Product (Vebeglogene Autotemcel) in Transfusion Dependent Beta-Thalassemia

🏥 Lantu Biopharma📍 2 sites📅 Started May 2024View details ↗
Phase 2RecruitingNCT06490627

Unraveling the Impact of Thalidomide at Diverse Doses in Transfusion Dependent Beta Thalassemia

🏥 National Institute of Blood and Marrow Transplant (NIBMT), Pakistan📍 1 site📅 Started Apr 2024View details ↗
Phase 1, PHASE2RecruitingNCT06280378

Β-Thalassemia Treatment with KL003 Cell Injection

👨‍⚕️ Haoquan Wu, PhD, R&D Kanglin Biotech📍 2 sites📅 Started Apr 2024View details ↗
RecruitingNCT06073860

A Post-Marketing Surveillance Study to Assess Safety of Luspatercept in Korean Patients With Myelodysplastic Syndrome or β-thalassemia

👨‍⚕️ Bristol-Myers Squibb, Bristol-Myers Squibb📍 2 sites📅 Started Mar 2024View details ↗
EARLY_Phase 1Enrolling by InvitationNCT06328764

CS-101 in Patients With β-thalassemia

👨‍⚕️ Yongrong Lai, M.D., First Affiliated Hospital of Guangxi Medical University📍 1 site📅 Started Mar 2024View details ↗
RecruitingNCT06271512

A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel

👨‍⚕️ Himal Lal Thakar, MD, bluebird bio, Inc.📍 6 sites📅 Started Jan 2024View details ↗
Phase 1RecruitingNCT06465550

A Phase 1 Study of Gene-modified Autologous Hematopoietic Stem Cell (BD211) Treating β-thalassemia Major

👨‍⚕️ Sujiang Zhang, M.D., Shanghai Ruijin Hospital, Shanghai Jiaotong University📍 3 sites📅 Started Jan 2024View details ↗
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