Advocacy intelligence hub — real-time data for patient organizations
Neurogene Inc. — PHASE1, PHASE2
Benjamin Greenberg — PHASE1
Northwell Health — NA
Emily de los Reyes
Jessica Scherr
Alcyone Therapeutics, Inc — PHASE1, PHASE2
Emily de los Reyes
University of Rochester
Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
FINANCIAL LANDSCAPE SUMMARY
Total programs
Travel grants
Travel Grants1
BioMarin Patient Assistance Program (Brineura)
Ronald G Crystal, MD, MD
Weill Medical College of Cornell University
📍 NEW YORK, NY
Forbes D Porter, M.D.
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
📍 Bethesda, Maryland
An N Dang Do, M.D.
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
📍 Bethesda, Maryland
Vicki J Swier
Pediatrics and Rare Diseases Group
Sara E Mole
Institute of Child Health and MRC Laboratory for Molecular Cell Biology and Great Ormond Street
Jon J Brudvig
Pediatrics & Rare Diseases Group