Autosomal dominant polycystic kidney disease type 1 with tuberous sclerosis Advocacy Hub | UniteRare

At a Glance

Live from database

Regulatory Watchboard

6 events

Sep 2026Assessing Changes in Multi-parametric MRI in Patients With Acute Demyelinating Lesions Taking Clemastine Fumarate as a Myelin Repair Therapy

University of California, San Francisco — PHASE1, PHASE2

TrialNOT YET RECRUITING

Mar 2026Sleep and Circadian Interventions for College Students at High Risk of Suicide

University of Pittsburgh — NA

TrialNOT YET RECRUITING

Mar 2026Safety, Tolerability, and Pharmacokinetics of SVG103 (Paxalisib) in Focal Cortical Dysplasia Type II (FCD-II), Tuberous Sclerosis Complex (TSC) or Hemimegalencephaly (HME)

Sovargen — PHASE1, PHASE2

TrialNOT YET RECRUITING

Dec 2025Sapu003 in Advanced mTOR-sensitive Solid Tumors

SAPU NANO (US) LLC — PHASE1

TrialRECRUITING

Jul 2024Astroscape: A Study of Radiprodil on Safety, Tolerability, Pharmacokinetics, and Effect on Seizures and Behavioral Symptoms in Patients With TSC or FCD Type II

GRIN Therapeutics, Inc. — PHASE1, PHASE2

TrialRECRUITING

May 2015Autism Spectrum Disorder (ASD) and Intellectual Disability (ID) Determinants in Tuberous Sclerosis Complex (TSC)

Boston Children's Hospital

TrialACTIVE NOT RECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

Total programs

No financial assistance programs currently listed for Autosomal dominant polycystic kidney disease type 1 with tuberous sclerosis.
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Clinical Trial Landscape

3 active trials

1Phase 1

1Unknown

1PHASE1, PHASE2

3Total recruiting

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Recent News & Research

No recent news articles indexed yet for Autosomal dominant polycystic kidney disease type 1 with tuberous sclerosis.
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Specialist Network

Top 6 by expertise

Darcy Krueger, MD, PhD, MD

Children's Hospital Medical Center, Cincinnati

📍 CINCINNATI, OH

Score 32 trials

Mustafa Sahin, MD, PhD, MD

Boston Children's Hospital

📍 BOSTON, MA

Score 35 trials

David N Franz

Children's Hospital Medical Center, Cincinnati

Score 01 trial

Nicole McDonald

University of California, Los Angeles

Score 01 trial

Shoufeng Li, Ph.D

Aucta Pharmaceuticals, Inc

Score 01 trial

Julian Sampson

Cardiff University

Score 01 trial

View all Autosomal dominant polycystic kidney disease type 1 with tuberous sclerosis specialists →

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