Autosomal dominant adult-onset proximal spinal muscular atrophy

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At a Glance

Live from database

14Recruiting trials

Regulatory Watchboard

10 events

Jan 2028Double-Blind Clinical Trial of Subthalamic Nucleus Deep Brain Stimulation in Early-Stage Parkinson's Disease

Mallory Hacker — NA

TrialNOT YET RECRUITING

Sep 2026A Study to Learn About the Safety and Effects of Salanersen (BIIB115) When Given to Babies With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Onasemnogene Abeparvovec

Biogen — PHASE3

TrialNOT YET RECRUITING

Jul 2026ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)

Novartis Pharmaceuticals — PHASE4

TrialNOT YET RECRUITING

Apr 2026A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam

Biogen — PHASE3

TrialNOT YET RECRUITING

Mar 2026Safety and Feasibility of a Self-Learning Bolus Calculator With Simplified Meal Announcement in Adolescents With Type 1 Diabetes Using Automated Insulin Delivery

Anas El Fathi — NA

TrialRECRUITING

Jan 2026The Effect of rTMS Over the SMA on Gait Performance in Parkinson's Disease

The Hong Kong Polytechnic University — NA

TrialNOT YET RECRUITING

Dec 2025prTMS as an Intervention for Bradykinesia in Parkinson's Disease

Danish Research Centre for Magnetic Resonance — NA

TrialRECRUITING

Sep 2025A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

Scholar Rock, Inc. — PHASE2

TrialRECRUITING

Sep 2025Safety, Usability, and Effectiveness of a Gait Exoskeleton for Children and Adolescents With Neurodevelopmental Disorders.

MarsiBionics — NA

TrialNOT YET RECRUITING

Jul 2025Study of the Reproducibility of the French Version of the Modified SMAFRS Scale

Institut de Myologie, France

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for Autosomal dominant adult-onset proximal spinal muscular atrophy.
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Clinical Trial Landscape

14 active trials

1Phase 2

8N/A

4Unknown

1PHASE1, PHASE2

14Total recruiting

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Recent News & Research

No recent news articles indexed yet for Autosomal dominant adult-onset proximal spinal muscular atrophy.
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Specialist Network

Top 6 by expertise

Eugenio Mercuri, MD

Istituto Gaslini

📍 Genova

Score 313 trials

Laurent Servais, MD

Centre Hospitalier Universitaire de Liege

Score 226 trials1 pub

Enrico Bertini, MD

Bambino Gesù Children's Hospital, Department of Neurosciences

Score 64 trials

Kenneth H Fischbeck, M.D., M.D

National Institute of Neurological Disorders and Stroke (NINDS)

📍 BETHESDA, MD

Score 46 trials

Richard S Bedlack, MD, PhD, M.D. Ph.D

Duke University

📍 DURHAM, NC

Score 42 trials

May Orfali, MD

Gemma Biotherapeutics

Score 43 trials

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