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9550+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 20 of 9550 recruiting trials

NAEnrolling by InvitationNCT06990178

Adaptive Neoadjuvant Therapy for Esophageal Cancer

👨‍⚕️ Tao Zhen Yu, MD, National Cancer Center/ Cancer Hospital &Shenzhen Hospital Chinese Academy of Medical Sciences and Peking Union Medical College📍 1 site📅 Started Mar 2028View details ↗
Phase 1RecruitingNCT05988463

Dose-Escalation Study of Artesunate Patients With IPF

👨‍⚕️ Joshua Mooney, MD, Stanford University📍 1 site📅 Started Jan 2027View details ↗
RecruitingNCT07483853

Reliability and Validation of the WB-MRI Radiological Score in CRMO

🏥 IRCCS Azienda Ospedaliero-Universitaria di Bologna📍 1 site📅 Started Jan 2027View details ↗
Phase 2RecruitingNCT07125183

Study on Efficacy and Tolerability of Weekly Doxorubicin in Elderly Patients With Advanced or Metastatic Leiomyosarcoma

👨‍⚕️ Breelyn Wilky, MD, University of Colorado, Denver📍 1 site📅 Started Dec 2026View details ↗
NARecruitingNCT05962346

Fetal Endoscopic Tracheal Occlusion for Congenital Diaphragmatic Hernia

👨‍⚕️ Mauro Schenone, MD, Mayo Clinic📍 1 site📅 Started Dec 2026View details ↗
RecruitingNCT06628687

A Study to Learn How BIIB141 (Omaveloxolone) Affects the Health of Participants With Friedrich's Ataxia Who Took it During Pregnancy and/or During Breastfeeding and About the Health of Their Babies

👨‍⚕️ Medical Director, Biogen📍 1 site📅 Started Oct 2026View details ↗
Phase 2RecruitingNCT07195734

Testing the Addition of Chemotherapy or Chemo-Immunotherapy to the Usual Surgery for Advanced Head and Neck Cancer

👨‍⚕️ Nabil F Saba, NRG Oncology📍 19 sites📅 Started Oct 2026View details ↗
EARLY_Phase 1RecruitingNCT07107659

Safety and Efficacy of ONT01 in Lupus

🏥 Hospital for Special Surgery, New York📍 1 site📅 Started Sep 2026View details ↗
Phase 2RecruitingNCT06980038

Testing Whether Cemiplimab (REGN2810) Plus CDX-1140 Given Prior to Surgery Are Better Than Cemiplimab (REGN2810) Alone in Patients With Stage III-IV Head and Neck Cancer

👨‍⚕️ Matin Imanguli, JHU Sidney Kimmel Comprehensive Cancer Center LAO📍 3 sites📅 Started Aug 2026View details ↗
Phase 2RecruitingNCT07097311

Study to Evaluate the Use of Triheptanoin in Patients With Medium Chain Acyl-CoA Dehydrogenase Deficiency (MCADD)

👨‍⚕️ Gerard Vockley, UPMC Children's Hospital of Pittsburgh📍 1 site📅 Started Jul 2026View details ↗
Phase 3RecruitingNCT07298447

Donidalorsen Treatment in Children With Hereditary Angioedema

🏥 Ionis Pharmaceuticals, Inc.📍 3 sites📅 Started Jul 2026View details ↗
Phase 1, PHASE2RecruitingNCT06965114

Testing the Combination of Anti-cancer Drugs, Tovorafenib Plus Rituximab, in Patients With Hairy Cell Leukemia

👨‍⚕️ Seema A Bhat, Ohio State University Comprehensive Cancer Center LAO📍 1 site📅 Started Jun 2026View details ↗
NARecruitingNCT07060534

Building Healthy Eating and Self-Esteem Together for University Students

👨‍⚕️ Kelsie Forbush, PhD, University of Kansas📍 1 site📅 Started Jun 2026View details ↗
NARecruitingNCT07371182

Luvometinib in Pediatric SS-LCH With Special-site Single/Multifocal Bone Lesions

🏥 West China Second University Hospital📍 11 sites📅 Started Jun 2026View details ↗
RecruitingNCT07488806

Natural History Study for Patients With Nemaline Myopathy in Spain

🏥 Hospital Universitari Vall d'Hebron Research Institute📍 1 site📅 Started Jun 2026View details ↗
Phase 1, PHASE2RecruitingNCT07398508

Phase I/II Study of NORTHERA (DROXIDOPA) for Dysautonomia in Pediatric Survivors of Menkes Disease.

👨‍⚕️ Stephen G Kaler, MD, MPH, Columbia University📍 1 site📅 Started Jun 2026View details ↗
Phase 2RecruitingNCT07249346

Dose-Expansion Study of Low Dose Post-Transplant Cyclophosphamide/Tacrolimus/Ruxolitinib for Graft-versus-Host Disease (GVHD) Prophylaxis in Myeloablative Allogeneic Peripheral Blood Stem Cell Transplantation

👨‍⚕️ Hannah Choe, MD, Ohio State University Comprehensive Cancer Center📍 1 site📅 Started Jun 2026View details ↗
Phase 1RecruitingNCT07171203

Neoadjuvant Imatinib and Fampridine in KIT Mutant Gastrointestinal Stromal Tumor

👨‍⚕️ Paul Fanta, MD, University of California, San Diego📍 1 site📅 Started Jun 2026View details ↗
NARecruitingNCT06828185

Patient Reported Experiences With Sparing External Oblique Fascia Vs Standard Inguinal Orchiectomy

🏥 Loma Linda University📍 1 site📅 Started May 2026View details ↗
Phase 2RecruitingNCT06987539

A Study to Evaluate the Pharmacokinetics, Pharmacodynamics, Safety and Tolerability of Inebilizumab in Children With Generalized Myasthenia Gravis (gMG)

👨‍⚕️ MD, Amgen📍 1 site📅 Started Apr 2026View details ↗
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