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10259+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 20 of 10259 recruiting trials

Phase 3RecruitingNCT06497465

Dolutegravir/Lamivudine Dual Therapy for ART-naïve People With HIV and TB Receiving Rifampin-based TB Treatment

👨‍⚕️ Ethel M Weld, MD, Johns Hopkins University📍 6 sites📅 Started Sep 2025View details ↗
RecruitingNCT07124000

DESTINY-PANTUMOUR04

🏥 AstraZeneca📍 15 sites📅 Started Sep 2025View details ↗
RecruitingNCT07339800

Chest CT Scan in Pulmonary Mucormycosis: Prognostic Value

🏥 University Hospital, Strasbourg, France📍 1 site📅 Started Sep 2025View details ↗
Phase 2RecruitingNCT07118254

A PHASE II PROSPECTIVE RANDOMIZED DOUBLE-MASKED CROSSOVER STUDY ASSESSING THE SAFETY & EFFICACY OF RHPRG4 (450 μG/ML RECOMBINANT HUMAN PROTEOGLYCAN 4) COMPARED TO VEHICLE FOR THE TREATMENT OF OCULAR GRAFT-VERSUS-HOST DISEASE (OGVHD)

🏥 Lubris Bio Pty Ltd📍 3 sites📅 Started Sep 2025View details ↗
RecruitingNCT07156149

Fabhalta Capsules Specified Drug-use Survey

👨‍⚕️ Novartis Pharmaceuticals, Novartis Pharmaceuticals📍 23 sites📅 Started Sep 2025View details ↗
Phase 2RecruitingNCT07118241

A PHASE II PROSPECTIVE RANDOMIZED DOUBLE-MASKED CONTROLLED STUDY ASSESSING THE SAFETY & EFFICACY OF RHPRG4 (450 µG/ML RECOMBINANT HUMAN PROTEOGLYCAN 4) COMPARED TO VEHICLE FOR THE TREATMENT OF SJÖGREN'S RELATED DRY EYE DISEASE

🏥 Lubris Bio Pty Ltd📍 6 sites📅 Started Sep 2025View details ↗
RecruitingNCT07251725

GEN-FPF: Genetic Exploration of Familial Pulmonary Fibrosis

🏥 Fondazione IRCCS Policlinico San Matteo di Pavia📍 1 site📅 Started Sep 2025View details ↗
Enrolling by InvitationNCT07448753

ACTG2/FLNA Testing Yield in Adult Idiopathic Chronic Intestinal Pseudo-Obstruction (CIPO) With Reduced/Absent Distal Esophageal Contractility

🏥 Marina Coletta📍 1 site📅 Started Sep 2025View details ↗
Phase 4RecruitingNCT07176689

Nirogacestat in Premenopausal Females With Desmoid Tumor/Aggressive Fibromatosis (DT/AF)

👨‍⚕️ Winette van der Graff, MD, The Netherlands Cancer Institute📍 20 sites📅 Started Sep 2025View details ↗
RecruitingNCT07053891

LUPKYNIS Drug-use Results Survey

🏥 Otsuka Pharmaceutical Co., Ltd.📍 1 site📅 Started Sep 2025View details ↗
Phase 2RecruitingNCT07159074

Repurposing Tilmanocept for Cardiac Sarcoidosis

👨‍⚕️ Ravi Karra, MD, Duke Health📍 1 site📅 Started Sep 2025View details ↗
NARecruitingNCT07163338

Prevalence and Consequences of Antiphospholipid Syndrome in Patients Aged 65 and Over With Ischemic Strokes (IS)

🏥 CHU de Reims📍 1 site📅 Started Sep 2025View details ↗
Phase 1RecruitingNCT07215650

Clinical Study of Cizutamig in Generalized Myasthenia Gravis (gMG)

🏥 Candid Therapeutics📍 1 site📅 Started Sep 2025View details ↗
RecruitingNCT07134387

Long-Term Burden of BPD and Health-Related Quality of Life (BronQ Family)

👨‍⚕️ Julia Feiler, Dr, Global Foundation for the Care of Newborn Infants (GFCNI)📍 1 site📅 Started Sep 2025View details ↗
Phase 1RecruitingNCT06589245

Inhaled Ciclesonide Study in Preterm Infants

👨‍⚕️ Venkatesh Sampath, MD, Children's Mercy Hospital Kansas City📍 1 site📅 Started Sep 2025View details ↗
Phase 4RecruitingNCT07045935

Metabolic Outcomes in Patients With Prolactinomas Under Dopamine Agonist Treatment

👨‍⚕️ Cihan Atila, Dr., University Hospital Basel, Dept. of Endocrinology, Metabolism & Diabetes📍 1 site📅 Started Sep 2025View details ↗
Phase 1, PHASE2RecruitingNCT07281781

Treating Anemia in Myelofibrosis With Repurposed Drugs (Nelfinavir) That Restore Iron Delivery to the Bone Marrow

👨‍⚕️ Angela Flesichman, MD, PhD, Chao Family Comprehensive Cancer Center📍 1 site📅 Started Sep 2025View details ↗
Phase 1RecruitingNCT06366230

Adding Urea to the Final Dialysis Fluid

👨‍⚕️ Ramin Sam, MD, Zuckerberg San Francisco General- UCSF📍 1 site📅 Started Sep 2025View details ↗
Phase 3RecruitingNCT07091630

A Study to Assess the Efficacy and Safety of Empasiprubart in Adults With CIDP

🏥 argenx📍 19 sites📅 Started Sep 2025View details ↗
Phase 2RecruitingNCT07225374

Cisplatin-Based Chemotherapy Followed by Maintenance Avelumab in UTUC

👨‍⚕️ SE HOON PARK, MD,PhD, SamsungMedicalCenter📍 1 site📅 Started Sep 2025View details ↗
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