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Showing 20 of 104 recruiting trials for “sickle-cell-beta-thalassemia-disease

Phase 3RecruitingNCT05477563

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

🏥 Vertex Pharmaceuticals Incorporated📍 6 sites📅 Started Aug 2022View details ↗
RecruitingNCT05153967

Cooperative Assessment of Late Effects for SCD Curative Therapies

👨‍⚕️ Michael R DeBaun, MD, MPH, Vanderbilt University Medical Center📍 5 sites📅 Started Jul 2022View details ↗
Phase 2RecruitingNCT05336201

Cognitive Remediation Intervention to Prepare for Transition of Care

🏥 University of Alabama at Birmingham📍 1 site📅 Started Jul 2022View details ↗
RecruitingNCT05170412

Dietary Intake and Dietary Behaviors in Adults With Sickle Cell Disease

👨‍⚕️ Nicole M Farmer, M.D., National Institutes of Health Clinical Center (CC)📍 1 site📅 Started May 2022View details ↗
NARecruitingNCT05210114

Cutaneous Hydration Assessment in SCD

👨‍⚕️ Enrico Novelli, MD, University of Pittsburgh📍 1 site📅 Started Jan 2022View details ↗
RecruitingNCT06213402

RADeep Multicenter European Epidemiological Platform for Patients Diagnosed With Rare Anemia Disorders (RADs)

👨‍⚕️ María del Mar Manú Pereira, PhD, Vall d'hebron Research Institute - Vall d'Hebron Research Institute - University Hospital Vall d'Hebrón (VHIR/HUVH)📍 1 site📅 Started Nov 2021View details ↗
Phase 2RecruitingNCT05012631

Losartan for Diffuse Myocardial Fibrosis in Sickle Cell Disease

🏥 Children's Hospital Medical Center, Cincinnati📍 1 site📅 Started Sep 2021View details ↗
NARecruitingNCT04484272

A Stress and Pain Self-management m-Health App for Adult Outpatients With Sickle Cell Disease

👨‍⚕️ Miriam O. Ezenwa, University of Florida📍 1 site📅 Started Apr 2021View details ↗
RecruitingNCT04416178

Sickle Cell Disease and the Genomic and Gene Therapy Needs of Stakeholders

👨‍⚕️ Liza M. Johnson, MD, MPH, MSB, St. Jude Children's Research Hospital📍 1 site📅 Started Dec 2020View details ↗
EARLY_Phase 1RecruitingNCT05745532

Safety and Efficacy Evaluation of β-globin Restored Autologous Hematopoietic Stem Cells in β-thalassemia Major Patients

👨‍⚕️ Chao Liu, PHD, Shenzhen Hemogen📍 1 site📅 Started Dec 2020View details ↗
Enrolling by InvitationNCT04628585

Long-term Follow-up of Subjects with Sickle Cell Disease Treated with Ex Vivo Gene Therapy

👨‍⚕️ Anjulika Chawla, MD, bluebird bio, Inc.📍 16 sites📅 Started Oct 2020View details ↗
NARecruitingNCT04688411

An mHealth Strategy to Improve Medication Adherence in Adolescents With Sickle Cell Disease

👨‍⚕️ Sherif M. Badawy, MD, MS, Ann & Robert H Lurie Children's Hospital of Chicago📍 1 site📅 Started Sep 2020View details ↗
NARecruitingNCT03976180

High-flow Oxygen for Vaso-occlusive Pain Crisis

👨‍⚕️ Armand Mekontso, Assistance Publique - Hôpitaux de Paris📍 1 site📅 Started Apr 2020View details ↗
Phase 1RecruitingNCT04055818

A Study of Nicotinamide With Oral Tetrahydrouridine and Decitabine to Treat High Risk Sickle Cell Disease

👨‍⚕️ Robert Molokie, University of Illinois at Chicago College of Medicine📍 1 site📅 Started Jan 2020View details ↗
Phase 2RecruitingNCT04143724

Study of Safety & PK of Luspatercept (ACE-536) in Pediatric Participants With Beta (β)-Thalassemia

👨‍⚕️ Bristol-Myers Squibb, Bristol-Myers Squibb📍 26 sites📅 Started Nov 2019View details ↗
RecruitingNCT05376046

Study of Erythrocyte Parameters and Hypercoagulability in Sickle Cell Disease (SCD-TGA)

🏥 BILLOIR📍 1 site📅 Started Sep 2018View details ↗
Phase 2RecruitingNCT03587272

Minimizing Toxicity in HLA-identical Sibling Donor Transplantation for Children With Sickle Cell Disease

👨‍⚕️ Robert Nickel, MD, Children's National Research Institute📍 7 sites📅 Started Apr 2018View details ↗
NARecruitingNCT03353584

Effect of Virtual Reality Technology for Pain Management of Vaso-Occlusive Crisis in Patients With Sickle Cell Disease

👨‍⚕️ Michael Frett, MD, St. Jude Children's Research Hospital📍 2 sites📅 Started Feb 2018View details ↗
Phase 2RecruitingNCT02675959

Myeloablative Conditioning, Prophylactic Defibrotide and Haplo AlloSCT for Patients With Sickle Cell Disease

👨‍⚕️ Mitchell Cairo, MD, New York Medical College📍 4 sites📅 Started Jul 2017View details ↗
Phase 1, PHASE2RecruitingNCT03128996

Reduced Intensity Conditioning and Familial HLA-Mismatched BMT for Non-Malignant Disorders

👨‍⚕️ Shalini Shenoy, MD, Washington University School of Medicine📍 4 sites📅 Started Mar 2017View details ↗
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