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10245+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 20 of 10245 recruiting trials

Phase 3RecruitingNCT07168161

BDB-001 Phase III Trial in ANCA-Associated Vasculitis

👨‍⚕️ Minghui Zhao, M.D., Peking University First Hospital📍 50 sites📅 Started Nov 2025View details ↗
Phase 3RecruitingNCT06983821

Safe Effective Therapy With Low-Dose Glucocorticoid in ANCA-Associated Vasculitis (SAFE-LOW)

👨‍⚕️ David Massicotte-Azarniouch, MD, MSc, The Ottawa Hospital📍 2 sites📅 Started Nov 2025View details ↗
NARecruitingNCT07300332

Exercise Training and Vitamin D Metabolism

👨‍⚕️ Dimitrios Draganidis, PhD, University of Thessaly📍 1 site📅 Started Nov 2025View details ↗
Phase 1RecruitingNCT07228364

Safety, Tolerability and Pharmacokinetics of AZD1613 in Adults With Autosomal Dominant Polycystic Kidney Disease

🏥 AstraZeneca📍 15 sites📅 Started Nov 2025View details ↗
Phase 2RecruitingNCT07123961

Pediatric Acute Respiratory Distress Syndrome (ARDS) Management Trial

👨‍⚕️ Nadir Yehya, MD, MSCE, Children's Hospital of Philadelphia📍 1 site📅 Started Nov 2025View details ↗
Phase 2RecruitingNCT07259928

Safety and Proof of Concept Study of ANXV (Annexin A5) in Patients With Diabetic Retinopathy or Retinal Vein Occlusion

👨‍⚕️ Anna Frostegård, MD, PhD, Annexin Pharmaceuticals AB📍 1 site📅 Started Nov 2025View details ↗
Phase 2RecruitingNCT07110844

Teclistamab-Daratumumab in AL Amyloidosis

👨‍⚕️ Suzanne Lentzsch, MD, PhD, Columbia University📍 1 site📅 Started Nov 2025View details ↗
NARecruitingNCT07428356

Histotripsy for Ablation of Liver Tumours in Asia

👨‍⚕️ Prof Brian Goh, MBBS, MMed, MSc, FRCSEd, FAMS, National Cancer Centre, Singapore📍 3 sites📅 Started Nov 2025View details ↗
RecruitingNCT07228793

Natural History Study of Patients With EYS-Associated RP

👨‍⚕️ Marianna Weener, MD, PhD, Oftalmic📍 1 site📅 Started Nov 2025View details ↗
Phase 2RecruitingNCT07110246

Dabrafenib and Trametinib for BRAF V600 Mutant Low-Grade Gliomas

👨‍⚕️ Sabine Mueller, MD, PHD, University of California, San Francisco📍 4 sites📅 Started Nov 2025View details ↗
RecruitingNCT06795893

The Anifrolumab PRIM Program

👨‍⚕️ Syd Philips, PPD Miami, US📍 1 site📅 Started Nov 2025View details ↗
EARLY_Phase 1RecruitingNCT04008121

Feasibility and Safety of MB-102 in Ocular Angiography as Compared to Fluorescein Sodium

👨‍⚕️ Richard B Dorshow, PhD, MediBeacon📍 1 site📅 Started Nov 2025View details ↗
NARecruitingNCT06823089

Early Feasibility Study of Cartilage Defect Repair

🏥 Cytex Therapeutics, Inc.📍 1 site📅 Started Nov 2025View details ↗
Phase 1RecruitingNCT07361094

Autologous CD19/BCMA Dual-Target CAR-T for Relapsed/Refractory Autoimmune Diseases

🏥 Beijing Boren Hospital📍 1 site📅 Started Nov 2025View details ↗
NARecruitingNCT07090226

Diffuse Cutaneous Scleroderma (DSSc) SFDI Study

👨‍⚕️ Andreea Bujor, MD, PhD, BU Chobanian & Advesian School of Medicine📍 1 site📅 Started Nov 2025View details ↗
RecruitingNCT07216053

Predictive Value of Lung Ultrasound for Respiratory Decompensation in Late Preterm Neonates

👨‍⚕️ Nicole Spillane, Hackensack Meridian Health📍 1 site📅 Started Nov 2025View details ↗
Phase 2RecruitingNCT07015242

A Study of the Efficacy and Safety of Lisocabtagene Maraleucel (Liso-cel) as First-Line Therapy in Adults With Transplant-Ineligible Primary Central Nervous System Lymphoma

👨‍⚕️ Bristol-Myers Squibb, Bristol-Myers Squibb📍 82 sites📅 Started Nov 2025View details ↗
NARecruitingNCT07373054

Umbilical Cord Mesenchymal Stem Cell-Derived Exosomes in the Treatment of Androgenic Alopecia

🏥 Fujian Medical University Union Hospital📍 1 site📅 Started Nov 2025View details ↗
NARecruitingNCT07293923

Magenta Elevate™ Clinical Feasibility Study in Cardiogenic Shock

👨‍⚕️ Yelena Lalazar, Magenta Medical📍 5 sites📅 Started Nov 2025View details ↗
Enrolling by InvitationNCT07212764

Mobile App-Based Infection Monitoring in Familial Mediterranean Fever

👨‍⚕️ Bengisu Menentoğlu, Istanbul University📍 1 site📅 Started Nov 2025View details ↗
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