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10153+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 20 of 10153 recruiting trials

RecruitingNCT06919484

The Physiological Effect of RCexp on Ventilation/Perfusion Distribution

🏥 Southeast University, China📍 1 site📅 Started Nov 2025View details ↗
Phase 3RecruitingNCT07441291

CD19 CAR-T vs DLI for Post-HSCT MRD in Ph- ALL: A RCT

🏥 Peking University People's Hospital📍 1 site📅 Started Nov 2025View details ↗
NARecruitingNCT07166848

Electrostimulation Study for Ocular Graft vs. Host Disease

👨‍⚕️ Zhonghui Luo, MD, PhD, Massachusetts Eye and Ear Infirmary📍 1 site📅 Started Nov 2025View details ↗
RecruitingNCT07252687

The Effect of Gender-affirmative Measures on Breast Perception in Trans Men

🏥 Medical University Innsbruck📍 1 site📅 Started Nov 2025View details ↗
Phase 2RecruitingNCT07296484

Trial Against INtractable Type 2 Diabetes (CAPTAIN-T2D)

🏥 Sparrow Pharmaceuticals📍 46 sites📅 Started Nov 2025View details ↗
Phase 3RecruitingNCT04851015

Low Dose Trimethoprim-Sulfamethoxazole for the Treatment of Pneumocystis Jirovecii Pneumonia

👨‍⚕️ Emily G McDonald, MD MSc, Research Institute of the McGill University Health Centre📍 1 site📅 Started Nov 2025View details ↗
NARecruitingNCT07286448

Personalized Digital Training for COGnitive FITness in Mild Cognitive Impairment

🏥 Giovanna Zamboni📍 1 site📅 Started Nov 2025View details ↗
RecruitingNCT07148193

Quality of Life and Medical Care of Long-term Sarcoma Survivors in Germany (PROSa+)

👨‍⚕️ Martin Eichler, Dr., TU Dresden & NCT/ UCC Dresden📍 5 sites📅 Started Nov 2025View details ↗
NARecruitingNCT06945081

Wilson's Disease Treated With D-Penicillamine: Characterization of Skin Damage Secondary to Treatment by Measuring Skin Elasticity

👨‍⚕️ JEAN-LUC PERROT, PHD, Service de Dermatologie, Hôpital Nord CHU de Saint-Étienne 42055 SAINT-ETIENNE Cedex 2📍 2 sites📅 Started Nov 2025View details ↗
RecruitingNCT07448935

One Gene, Two Diseases: the Pathologic Role of IGLV1-44 in AL Amyloidosis and POEMS

🏥 Fondazione IRCCS Policlinico San Matteo di Pavia📍 1 site📅 Started Nov 2025View details ↗
NARecruitingNCT07006649

CHOPXE - Analysis of Choriocapillaris Flow Deficits in Patients With Pseudoxanthoma Elasticum

👨‍⚕️ Laurie MOUROZEAU, Doctor, University Hospital, Angers📍 1 site📅 Started Nov 2025View details ↗
NARecruitingNCT07101770

A Prediction Model in Pregnant Women With Aplastic Anemia

👨‍⚕️ Xiaohui Zhang, MD, Peking University People's Hospital📍 1 site📅 Started Nov 2025View details ↗
Phase 3RecruitingNCT06994845

Study to Assess the Efficacy, Pharmacokinetics, Safety and Tolerability of Iptacopan in Pediatric Patients With Primary IgAN

👨‍⚕️ Novartis Pharmaceuticals, Novartis Pharmaceuticals📍 14 sites📅 Started Nov 2025View details ↗
Phase 4RecruitingNCT07457060

Phase IV Clinical Study of Sequential Vaccination of Sabin Strain and Wild Strain Inactivated Poliovirus Vaccine

🏥 Sinovac Biotech Co., Ltd📍 3 sites📅 Started Nov 2025View details ↗
Phase 2RecruitingNCT07189065

A Study of Rocbrutinib in Participants With Relapse or Refractory Non-GCB Diffuse Large B-Cell Lymphoma

🏥 Guangzhou Lupeng Pharmaceutical Company LTD.📍 41 sites📅 Started Nov 2025View details ↗
Phase 3RecruitingNCT06930625

A Study to Assess the Efficacy and Safety of Debio 4126 in Participants With Acromegaly Previously Treated With Somatostatin Analogs

🏥 Debiopharm International SA📍 71 sites📅 Started Nov 2025View details ↗
Phase 2RecruitingNCT07160608

Safety and Efficacy of Tarperprumig in Adult Participants With Anti-Neutrophil Cytoplasmic Antibody (ANCA)-Associated Vasculitis

🏥 Alexion Pharmaceuticals, Inc.📍 78 sites📅 Started Nov 2025View details ↗
NARecruitingNCT07334678

TROPIS Versus Coring Out Fistulectomy in High Anal Fistula

👨‍⚕️ Haitham M.Azmy Basiouny, Lecturer, Cairo University📍 1 site📅 Started Nov 2025View details ↗
Enrolling by InvitationNCT07450664

Observational Study of VYKAT™ XR in Patients With Prader-Willi Syndrome

🏥 Soleno Therapeutics, Inc.📍 2 sites📅 Started Nov 2025View details ↗
RecruitingNCT07411963

Evaluation of the Condition of Patients Receiving EARLY Ravulizumab and Admitted in ICU for gMG Crisis

🏥 Centre Hospitalier Universitaire de Nice📍 1 site📅 Started Nov 2025View details ↗
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