🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

Find Clinical Trials for Your Rare Disease

104+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

Clinical trial records are synced from ClinicalTrials.gov.
Report missing data
Clear

Showing 20 of 104 recruiting trials for “sickle-cell-beta-thalassemia-disease

NARecruitingNCT06219239

Safety and Efficacy of the Lentiviral Vector in Gene Therapy of Beta-thalassemia Patients

🏥 Institute of Hematology & Blood Diseases Hospital, China📍 1 site📅 Started Jan 2024View details ↗
Phase 2RecruitingNCT07292259

Combination of Thalidomide and Hydroxyuria in Transfusion Dependent Thalasemmia

👨‍⚕️ Tariq Ghafoor, FCPS,FRCP, National Institute of Blood and Marrow Transplant (NIBMT), Pakistan📍 9 sites📅 Started Jan 2024View details ↗
NARecruitingNCT06074198

Sickle Cell Children's Exercise Study (SuCCESs)

🏥 University of Maryland, Baltimore📍 2 sites📅 Started Nov 2023View details ↗
NARecruitingNCT05773729

Safety and Efficacy of Gene Modified Autologous Hematopoietic Stem Cells to Treat Transfusion-dependent Beta-thalassemia

👨‍⚕️ Chen Jing, M.D., Shanghai Children's Medical Center📍 1 site📅 Started Sep 2023View details ↗
Phase 2RecruitingNCT05693909

A Trial Testing SP-420 in Subjects With Transfusion-dependent β-thalassemia or Low-risk Myelodysplastic Syndromes

👨‍⚕️ Pharmacosmos Clinical and non-clinical Department, Pharmacosmos A/S📍 1 site📅 Started Sep 2023View details ↗
Phase 2RecruitingNCT05953584

A Phase 2 Open-label Study to Evaluate the Activity of Etavopivat on Transcranial Doppler Velocities in Pediatric Patients With Sickle Cell Disease Who Are at Increased Risk for Primary Stroke

👨‍⚕️ Clinical Transparency (dept. 2834), Novo Nordisk A/S📍 9 sites📅 Started Jun 2023View details ↗
Phase 4RecruitingNCT05730205

Effects of the Contraceptive Implant in Women With Sickle Cell Disease

🏥 University of Pennsylvania📍 1 site📅 Started Jun 2023View details ↗
RecruitingNCT06385886

Recruitment and Engagement in Care to Impact Practice Enhancement (RECIPE) for Sickle Cell Disease

👨‍⚕️ Julie Kanter, MD, University of Alabama, Birmingham (UAB)📍 9 sites📅 Started Jun 2023View details ↗
RecruitingNCT05991336

Growth and Development-related Outcomes in Children With Transfusion-dependent Beta-thalassemia After Gene Therapy

🏥 Institute of Hematology & Blood Diseases Hospital, China📍 1 site📅 Started Jun 2023View details ↗
RecruitingNCT05810181

Gene Therapy Communication: Use of a Needs Assessment to Drive Decision-AIDS for Gene Therapy for Rare Diseases (GENETX)

👨‍⚕️ Liza-Marie Johnson, MD, MPH, MSB, St. Jude Children's Research Hospital📍 1 site📅 Started Jun 2023View details ↗
Phase 2RecruitingNCT05640271

Tocilizumab for Acute Chest Syndrome

👨‍⚕️ Austin Wesevich, MD, University of Chicago📍 1 site📅 Started Apr 2023View details ↗
Phase 3RecruitingNCT05392894

RElated Haplo-DonoR Haematopoietic stEm Cell Transplantation for Adults With Severe Sickle Cell Disease

👨‍⚕️ Ann-Marie Murtagh, King's College Hospitals NHS Foundation Trust📍 1 site📅 Started Feb 2023View details ↗
EARLY_Phase 1RecruitingNCT05762510

A Study Evaluating the Safety and Efficacy of LentiRed Drug Product in Transfusion-dependent β-Thalassemia [TDT]

🏥 First Affiliated Hospital of Guangxi Medical University📍 1 site📅 Started Feb 2023View details ↗
Phase 2RecruitingNCT05736419

A Study of Immune Suppression Treatment for People With Sickle Cell Disease or β-Thalassemia Who Are Going to Receive an Allogeneic Hematopoietic Cell Transplantation (HCT)

👨‍⚕️ Maria Cancio, MD, Memorial Sloan Kettering Cancer Center📍 6 sites📅 Started Feb 2023View details ↗
RecruitingNCT05748717

Arterial Function Parameters and Transcranial Doppler Velocity in Paediatric Patients With Sickle Cell Disease

🏥 The University of The West Indies📍 1 site📅 Started Feb 2023View details ↗
Phase 2RecruitingNCT06198712

A Study to Evaluate the Pharmacokinetics and Safety of Etavopivat in Pediatric Patients With Sickle Cell Disease

👨‍⚕️ Clinical Transparency (dept. 2834), Novo Nordisk A/S📍 18 sites📅 Started Jan 2023View details ↗
Phase 1RecruitingNCT04925492

PET Imaging of Vaso-Occlusive Crisis (VOC) in SCD

👨‍⚕️ Enrico Novelli, MD, MS, University of Pittsburgh📍 1 site📅 Started Nov 2022View details ↗
Phase 1, PHASE2Enrolling by InvitationNCT05577312

Safety and Efficacy Evaluation of BRL-101 in Subjects With Transfusion-Dependent β-Thalassemia

👨‍⚕️ Xiaochen Wang, PhD, Bioray Laboratories📍 4 sites📅 Started Nov 2022View details ↗
RecruitingNCT05799118

Study of the Role of Genetic Modifiers in Hemoglobinopathies

👨‍⚕️ Petros Kountouris, PhD, Cyprus Institute of Neurology and Genetics📍 26 sites📅 Started Oct 2022View details ↗
RecruitingNCT05508932

Atrial Fibrillation in Beta-Thalassemia

🏥 University Hospital of Ferrara📍 1 site📅 Started Sep 2022View details ↗
← PreviousPage 4 of 6Next →

Get alerts when new trials open

Create a free account to follow conditions and receive trial notifications.

Create free account →