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11619+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 20 of 11619 recruiting trials

NARecruitingNCT06578104

PULSED AF Post-Approval Study

👨‍⚕️ Khaldoun Tarakji, MD, Medtronic CAS Chief Medical Officer📍 16 sites📅 Started Nov 2024View details ↗
RecruitingNCT06298565

A Non-interventional, Post-authorisation Safety Study of Patients Treated With Efgartigimod Alfa

🏥 argenx📍 35 sites📅 Started Nov 2024View details ↗
NARecruitingNCT06523361

Contribution of Immersive Virtual Reality to a Standardized Rehabilitation Program for Upper Limb Chronic Pain: A Single-Case Experimental Design Study

🏥 University Hospital, Angers📍 2 sites📅 Started Nov 2024View details ↗
NARecruitingNCT06614777

Characterization of the Cytokine Profile and the Microbiome in Darier's Disease

👨‍⚕️ Juliette Mazereeuw-hautier, MD, University Hospital of Toulouse📍 1 site📅 Started Nov 2024View details ↗
RecruitingNCT06645899

Institution of an Italian Multicenter Database of Patients Affected by Hypoparathyroidism or Pseudohypoparathyroidism

🏥 F.I.R.M.O. - Fondazione Italiana Ricerca sulle Malattie dell'Osso - Ente del Terzo Settore📍 41 sites📅 Started Nov 2024View details ↗
Phase 2RecruitingNCT06488313

A Study to Evaluate the Pharmacodynamics and Safety of ARCT-810 in Participants With OTCD

🏥 Arcturus Therapeutics, Inc.📍 1 site📅 Started Nov 2024View details ↗
RecruitingNCT07036874

Non-invasive Assessment for Outcome Prediction in Patients With Hepatocellular Carcinoma

👨‍⚕️ Jimmy CT Lai, MB ChB, Chinese University of Hong Kong📍 1 site📅 Started Nov 2024View details ↗
NARecruitingNCT07099456

Fertility And Sexual Function In CAH: CALLIOPE

👨‍⚕️ Andrea M Isidori, MD, PhD, FRCP📍 1 site📅 Started Nov 2024View details ↗
NARecruitingNCT06563674

Acceptance-based Healthy Lifestyles Program for Patients With Pneumoconiosis

🏥 Chinese University of Hong Kong📍 1 site📅 Started Nov 2024View details ↗
RecruitingNCT06657846

HRQoL and Financial Toxicity in Patients With VEXAS Syndrome

🏥 Gruppo Italiano Malattie EMatologiche dell'Adulto📍 17 sites📅 Started Nov 2024View details ↗
RecruitingNCT06644144

P4O2 ILD Extension

👨‍⚕️ Esther Nossent, MD, Amsterdam UMC, locatie VUmc📍 1 site📅 Started Nov 2024View details ↗
NARecruitingNCT06023472

Microfluidic Chip vs Density Gradient Centrifugation on the Euploidy Rate of Pre-implantation Genetic Testing

🏥 Professor Ernest Hung-Yu Ng📍 1 site📅 Started Nov 2024View details ↗
Phase 2RecruitingNCT06646497

Indication of HSCT in Patients With Refractory/Relapse AA After First-line Standard Immunosuppressive Therapy Aged More Than 40 Years

🏥 Assistance Publique - Hôpitaux de Paris📍 1 site📅 Started Nov 2024View details ↗
Phase 3RecruitingNCT06635720

REduced-dose Steroid PrOtocol for Childhood Nephrotic SyndromE (RESPONSE)

👨‍⚕️ Rulan Parekh, MD MS, The Hospital for Sick Children📍 1 site📅 Started Nov 2024View details ↗
Phase 1RecruitingNCT06631391

Phase I Study of Umbilical Cord Blood Natural Killer (NK) Cell Therapy for Children With High-risk, R/R Neuroblastoma.

👨‍⚕️ Yizhuo Zhang, SunYat Sen University Cancer Center📍 2 sites📅 Started Nov 2024View details ↗
RecruitingNCT06705036

Differential Study of Invasive Pituitary Adenomas in the Sellar and Cavernous Sinus Regions

👨‍⚕️ Tao Xie, Fudan University📍 1 site📅 Started Nov 2024View details ↗
Phase 2RecruitingNCT06709417

A Phase II Clinical Study of Sintilimab Combined with Chemotherapy Followed by Concurrent Chemoradiotherapy for Locally Advanced Unresectable Esophageal Squamous Cell Carcinoma (ESCC) (NICE-CS)

🏥 Shanghai Chest Hospital📍 1 site📅 Started Nov 2024View details ↗
RecruitingNCT06727669

Longitudinal Cohort of Thrombosis and Hemostasis Diseases

👨‍⚕️ Xiao-Hui Zhang, MD, Peking University Institute of Hematology, Peking University People's Hospital📍 5 sites📅 Started Nov 2024View details ↗
Phase 3RecruitingNCT06676449

TDLN-sparing RT Plus Immunotherapy and Chemotherapy in Locally Advanced ESCC

🏥 Fudan University📍 1 site📅 Started Nov 2024View details ↗
RecruitingNCT06742073

Histiocytosis and Inflammatory Manifestations in Patients with H Syndrome

👨‍⚕️ Sarah Elitzur, MD, Schneider Children'ds Medical Center📍 1 site📅 Started Nov 2024View details ↗
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