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Showing 20 of 104 recruiting trials for “sickle-cell-beta-thalassemia-disease

NARecruitingNCT06880679

Ultrasound Acute Chest Syndrome Sickle Cell Disease

👨‍⚕️ Seethal Jacob, MD, Indiana University📍 1 site📅 Started Apr 2025View details ↗
Phase 2RecruitingNCT05519111

Cannabinoids for the Reduction of Inflammation and Sickle Cell Related Pain

👨‍⚕️ Susanna Curtis, MOUNT SINAI HOSPITAL📍 1 site📅 Started Apr 2025View details ↗
NARecruitingNCT06853158

MULTIsite Feasibility of MUSIc Therapy to Address Quality Of Life in Sickle Cell Disease

👨‍⚕️ Jeffery A Dusek, PhD, University of California, Irvine📍 2 sites📅 Started Apr 2025View details ↗
RecruitingNCT06887907

Phenotypic and Transcriptomic Description of Megakaryocytes in Sickle Cell Patient

👨‍⚕️ Pierre COUGOUL, MD, University Hospital, Toulouse📍 1 site📅 Started Mar 2025View details ↗
Phase 3RecruitingNCT06612268

A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell Disease

👨‍⚕️ Clinical Transparency (dept. 2834), Novo Nordisk A/S📍 20 sites📅 Started Feb 2025View details ↗
Enrolling by InvitationNCT06685536

A Long-term Follow-up Study in Participants Who Received CS-101

👨‍⚕️ Yongrong Lai, M.D., First Affiliated Hospital of Guangxi Medical University📍 1 site📅 Started Jan 2025View details ↗
NARecruitingNCT06650813

Adapting the FACETS Program to Sickle Cell Disease

👨‍⚕️ Marie-Claire GAY, Pr, Paris Nanterre University📍 2 sites📅 Started Jan 2025View details ↗
Phase 1RecruitingNCT06772766

A Multiple Ascending Dose Study of 9MW3011 in Patients With Non-transfusion-dependent β-thalassemia

🏥 Mabwell (Shanghai) Bioscience Co., Ltd.📍 2 sites📅 Started Dec 2024View details ↗
Phase 2RecruitingNCT06635902

Intravenous L-Citrulline for Vaso-occlusive Pain Episode in Sickle Cell Disease

👨‍⚕️ Suvankar Majumdar, MD, Children's National Research Institute📍 1 site📅 Started Dec 2024View details ↗
NARecruitingNCT05383911

Empowering Adolescents and Young Adults With Sickle Cell Disease as Partners in Treatment Decision Making (EMPOWER-AYA)

🏥 Nemours Children's Clinic📍 1 site📅 Started Nov 2024View details ↗
Phase 1RecruitingNCT06442761

SCD Stem Cell Mobilization and Apheresis Using Motixafortide

👨‍⚕️ Alexis Leonard, MD, St. Jude Children's Research Hospital📍 2 sites📅 Started Nov 2024View details ↗
NARecruitingNCT06184126

Virtual Reality Devices as an Adjunct to Usual Care for Patients With Sickle Cell Disease Experiencing Vaso-Occlusive Crises

👨‍⚕️ R. Gentry Wilklerson, MD, U of Maryland, Baltimore📍 1 site📅 Started Nov 2024View details ↗
Phase 3RecruitingNCT06439082

A Study to Investigate the Efficacy and Safety of Crizanlizumab (5 mg/kg) Compared With Placebo in Adolescent and Adult Sickle Cell Disease Patients Who Experience Frequent Vaso-Occlusive Crises (SPARKLE)

🏥 Novartis Pharmaceuticals📍 30 sites📅 Started Oct 2024View details ↗
NARecruitingNCT06734520

Clinical Study of Super Transplantation in the Treatment of Severe β-thalassemia

👨‍⚕️ Hua Jiang, PHD, Guangzhou Medical University Affiliated Women's and Children's Medical Center📍 2 sites📅 Started Oct 2024View details ↗
Phase 2RecruitingNCT06421636

A Study to Test the Safety, Tolerability, and Efficacy of an Antibody, REGN7999, Injected Under the Skin for the Treatment of Iron Overload in Adult Participants With Non-Transfusion Dependent β-thalassemia, Using MRI Scans to Measure Iron Levels in the Body

👨‍⚕️ Clinical Trial Management, Regeneron Pharmaceuticals📍 26 sites📅 Started Sep 2024View details ↗
NARecruitingNCT07001631

Effect of EMDR for Reduction of Pain Interference in Children With Sickle Cell Disease

👨‍⚕️ Karin Fijnvandraat, prof. dr., Amsterdam UMC📍 1 site📅 Started Sep 2024View details ↗
Phase 1, PHASE2RecruitingNCT04774536

Transplantation of Clustered Regularly Interspaced Short Palindromic Repeats Modified Hematopoietic Progenitor Stem Cells (CRISPR_SCD001) in Patients with Severe Sickle Cell Disease

👨‍⚕️ Mark Walters, MD, UCSF Benioff Children's Hospital Oakland📍 2 sites📅 Started Sep 2024View details ↗
Phase 4RecruitingNCT06606886

Effects of Hydroxyurea and Metformin in Transfusion Dependent Beta-Thalassemia

👨‍⚕️ Ayesha Khan, MBBS MPhil, Bahria University Islamabad📍 1 site📅 Started Sep 2024View details ↗
RecruitingNCT06477289

Peripheral Arterial Tonometry and Neurocognition in Sickle Cell Disease

👨‍⚕️ Andrew Heitzer, Phd, St. Jude Children's Research Hospital📍 1 site📅 Started Sep 2024View details ↗
NARecruitingNCT06773715

Virtual Reality As Adjunct Therapy for Vaso-Occlusive Pain

🏥 Louisiana State University Health Sciences Center in New Orleans📍 1 site📅 Started Sep 2024View details ↗
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