Showing 20 of 47 recruiting trials for “fabry-disease”
Evaluation of the Safety, Tolerability and Efficacy of a Gene Therapy Drug for the Treatment of Pediatric Fabry Disease
👨⚕️ Hong Xu, MD,PhD, Children's Hospital of Fudan University📍 1 site📅 Started Feb 2024View details ↗
High-intensity Interval Training in Patients With Spinal Muscular Atrophy
A Head-to-head Study Comparing the Functional Value of Two Models of Robotically Assisted Rehabilitation in SMA (Spinal Muscular Atrophy) Patients
👨⚕️ Marek Jóźwiak, Wiktor Dega University Orthopedic and Rehabilitation Hospital📍 1 site📅 Started Dec 2023View details ↗
RecruitingNCT05994950 ↗
A Review of the Management and Outcomes of Children With SMA in the West Midlands During 2017-2022
🏥 Robert Jones and Agnes Hunt Orthopaedic and District NHS Trust📍 2 sites📅 Started Dec 2023View details ↗
Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
Study of the Safety and Biologic Activity of AL01211 in Treatment Naive Males With Classic Fabry Disease
German Observational Multicenter Study of Patients With Fabry Disease Under Enzyme Replacement Therapy With Pegunigalsidase-alfa
Biomarkers and Cardiac Imaging Diagnostic Assay for Monitoring Patients With Fabry Disease
T1 Mapping in Fabry Disease
Study to Evaluate the Safety, PK, PD, and Efficacy of PRX-102 in Japanese Patients With Fabry Disease
RecruitingNCT06610019 ↗
Cardiovascular Multimodality Imaging Study
Evaluate the Safety and Efficacy of Fabagal® (Agalsidase Beta) in Patients With Fabry Disease
Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 1 Patients
A Study of Replagal in Children and Adults With Fabry Disease in India
4D-310 in Adults With Fabry Disease and Cardiac Involvement
Italian Anderson Fabry Disease Cardiovascular Registry
👨⚕️ Elena Biagini, MD, PhD, IRCCS Azienda Ospedaliero-Universitaria di Bologna📍 20 sites📅 Started Jan 2022View details ↗
Outpatient Rehabilitation Intervention for Young Children With SMA
Enrolling by InvitationNCT05039866 ↗
Long-Term Follow-up of Subjects Who Were Treated With ST-920
Fabry Cardiomyopathy: Identification of Early Myocardial Structural and Tissue Abnormalities Using Multiparametric MRI
Long Duration Holter ECG in Fabry Disease
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