🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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Showing 4 of 24 recruiting trials for “Paroxysmal nocturnal hemoglobinuria

Phase 3RecruitingNCT05744921

A Study in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) to Evaluate How Safe Long-term Treatment With Pozelimab + Cemdisiran Combination Therapy is and How Well it Works

👨‍⚕️ Clinical Trial Management, Regeneron Pharmaceuticals📍 43 sites📅 Started Mar 2023View details ↗
Phase 3RecruitingNCT05133531

A Study to Evaluate How Safe Pozelimab + Cemdisiran Combination Therapy is and How Well it Works in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Who Have Not Recently Received or Have Not Received Complement Inhibitor Treatment

👨‍⚕️ Clinical Trial Management, Regeneron Pharmaceuticals📍 69 sites📅 Started Aug 2022View details ↗
NARecruitingNCT05755867

Global PNH Patient Registry

👨‍⚕️ Alice Houk, MS, Aplastic Anemia and MDS International Foundation📍 1 site📅 Started May 2021View details ↗
Phase 2RecruitingNCT04901936

A Study of Pegcetacoplan in Pediatric Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

🏥 Apellis Pharmaceuticals, Inc.📍 12 sites📅 Started Feb 2021View details ↗
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