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10439+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 20 of 10439 recruiting trials

Phase 1RecruitingNCT06915753

Safety and Preliminary Anti-Tumor Activity of TYRA-430 in Advanced Hepatocellular Carcinoma and Other Solid Tumors With Activating FGF/FGFR Pathway Aberrations

👨‍⚕️ Doug Warner, MD, Tyra Biosciences, Inc📍 16 sites📅 Started Apr 2025View details ↗
RecruitingNCT06962072

Outcomes Following Limb Sparing Surgery for Soft Tissue Sarcoma

🏥 Amsterdam UMC📍 1 site📅 Started Apr 2025View details ↗
NARecruitingNCT06852612

Dietary Treatment Strategies and Metabolic Control in Glycogen Storage Disease Type I

👨‍⚕️ Michel Hochuli, MD, PhD, Department of Diabetes, Endocrinology, Nutritional Medicine and Metabolism📍 1 site📅 Started Apr 2025View details ↗
RecruitingNCT06830499

Sapien 3 Transcatheter Aortic Valve Replacement in Young Aortic Valve Stenosis Patients From China

👨‍⚕️ Jian Yang, MD, PhD, Department of Cardiovascular Surgery of Xijing Hospital, Air Force Military Medical University📍 4 sites📅 Started Apr 2025View details ↗
NARecruitingNCT06845501

Purine Supplementation in Patients With AICA-Ribosiduria

👨‍⚕️ Francis RAMOND, doctor of medicine, Centre Hospitalier Universitaire de Saint Etienne📍 1 site📅 Started Apr 2025View details ↗
Phase 3RecruitingNCT06929624

A Phase 3 Clinical Study of SHR-A1912 Combined With R-GemOx Versus R-GemOx in Diffuse Large B-cell Lymphoma

🏥 Suzhou Suncadia Biopharmaceuticals Co., Ltd.📍 2 sites📅 Started Apr 2025View details ↗
NARecruitingNCT06956027

Ultrasound Features of Dupuytren's Disease

👨‍⚕️ Ilse Degreef, Prof. Dr., Universitaire Ziekenhuizen KU Leuven📍 1 site📅 Started Apr 2025View details ↗
NARecruitingNCT06955897

Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA

👨‍⚕️ Jacqueline Montes, Pt, EdD, Columbia University📍 1 site📅 Started Apr 2025View details ↗
RecruitingNCT06861309

Placental Imaging Techniques

👨‍⚕️ Megan D Whitham, MD, Carilion Clinic📍 1 site📅 Started Apr 2025View details ↗
Phase 1RecruitingNCT06747390

Intratumoral Lidocaine Injection Before Oropharyngeal Cancer Surgery

👨‍⚕️ Ryan Carey, MD, University of Pennsylvania📍 1 site📅 Started Apr 2025View details ↗
NARecruitingNCT06939660

BCI-Assisted SCS-EXS for Gait Optimization

🏥 Xuanwu Hospital, Beijing📍 1 site📅 Started Apr 2025View details ↗
Phase 1RecruitingNCT06047886

UAB 2419-CD34 Selection Using the Automated CliniMACS Prodigy

🏥 University of Alabama at Birmingham📍 1 site📅 Started Apr 2025View details ↗
RecruitingNCT06669949

Natural History of Sphingosine Phosphate Lyase Insufficiency Syndrome (SPLIS)

👨‍⚕️ Julie D Saba, MD, PhD, University of California, San Francisco📍 1 site📅 Started Apr 2025View details ↗
Phase 4RecruitingNCT07314281

Meropenem vs Azithromycin Efficacy in Case XDR Enteric Fever

👨‍⚕️ muhammad hamid, Indus Hospital and Health Network📍 1 site📅 Started Apr 2025View details ↗
Phase 2RecruitingNCT06854003

BRAZAN: A Randomized Phase 2 Study of Bendamustine, Rituximab, Cytarabine (AraC) Induction With Zanubrutinib (BRAZAN) Followed by Zanubrutinib/Rituximab +/- Sonrotoclax Maintenance in Treatment-Naïve Mantle Cell Lymphoma

👨‍⚕️ Christine Ryan, MD, Dana-Farber Cancer Institute📍 7 sites📅 Started Apr 2025View details ↗
NARecruitingNCT06713668

Augmented Pacing for Shock in the Cardiac Intensive Care Unit

🏥 Vanderbilt University Medical Center📍 1 site📅 Started Apr 2025View details ↗
Phase 2, PHASE3Enrolling by InvitationNCT06873035

An Interventional Study of Infigratinib in Children With Hypochondroplasia

🏥 QED Therapeutics, a BridgeBio company📍 22 sites📅 Started Apr 2025View details ↗
RecruitingNCT06850038

A Study Observing the Long-term, Effectiveness and Safety of Odevixibat (Bylvay) in Patients With Alagille Syndrome (ALGS) Who Are Receiving Ongoing Treatment

👨‍⚕️ Ipsen Medical, Director, Ipsen📍 8 sites📅 Started Apr 2025View details ↗
Phase 1, PHASE2RecruitingNCT06704269

Study to Assess Safety, Efficacy, and Cellular Kinetics of YTB323 in Generalized Myasthenia Gravis

👨‍⚕️ Novartis Pharmaceuticals, Novartis Pharmaceuticals📍 10 sites📅 Started Apr 2025View details ↗
Phase 2RecruitingNCT07077551

NALIRIFOX as Second-Line Chemotherapy in Extrapulmonary High-grade Neuroendocrine Neoplasms: a Prospective, Single-center, Single-arm Trial

🏥 Second Affiliated Hospital, School of Medicine, Zhejiang University📍 1 site📅 Started Apr 2025View details ↗
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