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9550+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 20 of 9550 recruiting trials

Phase 2RecruitingNCT07331155

A Phase II Clinical Study of LBL-024 Combination Therapy in Patients With Advanced Solid Tumour[Substudy 03(ESCC)]

👨‍⚕️ Lin Shen, Peking University Cancer Hospital & Institute📍 7 sites📅 Started Feb 2026View details ↗
Phase 2, PHASE3RecruitingNCT07454837

Phase 2b/3 Study to Evaluate Switching to Brelovitug for the Treatment of CHD in Participants Receiving Bulevirtide

🏥 Mirum Pharmaceuticals, Inc.📍 7 sites📅 Started Feb 2026View details ↗
RecruitingNCT07215975

A Real-World Study to Evaluate Luspatercept in Adults With Transfusion-Dependent Beta-Thalassemia in the Middle East

👨‍⚕️ Bristol Myers Squibb, Bristol-Myers Squibb📍 2 sites📅 Started Feb 2026View details ↗
NARecruitingNCT07073963

Virtual Patient Groups for Sarcoidosis Associated Fatigue

👨‍⚕️ Logan J Harper, MD, The Cleveland Clinic📍 1 site📅 Started Feb 2026View details ↗
Phase 2RecruitingNCT07103746

Ublituximab in Autoantibody Positive Immune Mediated Necrotizing Myopathy

👨‍⚕️ Julie Paik, M.D., M.H.S., Johns Hopkins Hospital: Division of Rheumatology📍 9 sites📅 Started Feb 2026View details ↗
Phase 1RecruitingNCT07433621

Quercetin in Patients With XIAP (X-linked Inhibitor of Apoptosis) Deficiency

👨‍⚕️ Rebecca Marsh, MD, Children's Hospital Medical Center, Cincinnati📍 1 site📅 Started Feb 2026View details ↗
NARecruitingNCT06544018

Circadian Rhythm Deregulation in Patients With CAPS

🏥 Hospices Civils de Lyon📍 6 sites📅 Started Feb 2026View details ↗
Phase 1, PHASE2RecruitingNCT07432867

Efficacy Safety Study of Gene Therapy for Sickle Cell DiseaseSCD Using Autologous CD34+ Cells Transduced ex Vivo, Carrying a Corrected Globin Gene and a Silencing RNA.

👨‍⚕️ Elisa MAGRIN, PhD, Department of Biotherapy, Necker-Enfants Malades Hospital📍 1 site📅 Started Feb 2026View details ↗
NARecruitingNCT07454174

Metabolic Impacts of Ren-Nu: A Dietary Program for Polycystic Kidney Disease

👨‍⚕️ Richard Fatica, MD, The Cleveland Clinic📍 1 site📅 Started Feb 2026View details ↗
Phase 1RecruitingNCT07471516

Zoledronic Acid Treatment in Patients With Congenital Dyserythropoietic Anemia

👨‍⚕️ Xin Zhao, MD📍 1 site📅 Started Feb 2026View details ↗
NARecruitingNCT07455864

Lysosomal Acid Lipase Deficiency in Risk Groups

👨‍⚕️ AstraZeneca Clinical Study Information Center📍 1 site📅 Started Feb 2026View details ↗
Phase 2RecruitingNCT07171905

CAT-VHL Exploring the Role of Carbonic Anhydrase IX as Diagnostic and Theranostic Target in Von-Hippel Lindau Disease

🏥 IRCCS Ospedale San Raffaele📍 1 site📅 Started Feb 2026View details ↗
EARLY_Phase 1RecruitingNCT06634628

iMagemHTT-009- FIH Evaluation of Novel Mutant Huntingtin PET Radioligand [11C]CHDI-00491009

🏥 CHDI Foundation, Inc.📍 1 site📅 Started Feb 2026View details ↗
Phase 2RecruitingNCT07104331

SARC046: A Phase II Trial of Nab-Sirolimus in Patients With Progressing or Symptomatic Epithelioid Hemangioendothelioma

🏥 Sarcoma Alliance for Research through Collaboration📍 6 sites📅 Started Feb 2026View details ↗
Phase 1RecruitingNCT07503808

A Study of IDE034 in Adult Participants With Locally Advanced/Metastatic Solid Tumors Types

🏥 IDEAYA Biosciences📍 5 sites📅 Started Feb 2026View details ↗
Phase 4RecruitingNCT06875960

A Study to Continue the Administration of Deucravacitinib in Participants With Systemic Lupus Erythematosus (SLE) or Discoid and/or Subacute Cutaneous Lupus Erythematosus (DLE/SCLE) Who Have Completed Study IM011074 or Study IM011132

👨‍⚕️ Bristol-Myers Squibb, Bristol-Myers Squibb📍 4 sites📅 Started Feb 2026View details ↗
Phase 1RecruitingNCT07148089

A Study of SGT-501 Gene Therapy in Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT)

🏥 Solid Biosciences Inc.📍 5 sites📅 Started Feb 2026View details ↗
NARecruitingNCT07406893

Reduction of Bacterial Seeding in Total Shoulder Arthroplasty

👨‍⚕️ Randall Otto, MD, St. Louis University📍 1 site📅 Started Feb 2026View details ↗
RecruitingNCT07303257

Quality of Life After Glaucoma Surgery: Evaluating the Patient Perspective Across Surgical Options

🏥 Hospices Civils de Lyon📍 1 site📅 Started Feb 2026View details ↗
Phase 1, PHASE2RecruitingNCT07189871

177Lu-BetaBart in Patients With Relapsed/Refractory, Locally Advanced Inoperable, or Metastatic Solid Tumors

🏥 Radiopharm Theranostics, Ltd📍 4 sites📅 Started Feb 2026View details ↗
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