Showing 19 of 19 recruiting trials for “x-linked-scapuloperoneal-muscular-dystrophy”
Safety and Preliminary Efficacy of ULSC in Facioscapulohumeral Muscular Dystrophy (FSHD)
👨⚕️ John W Day, MD, PhD, Stanford University, School of Medicine, Neuromuscular Research Division📍 1 site📅 Started Dec 2025View details ↗
A Study to Evaluate Del-brax (Also Referred to as AOC 1020) in Participants With FSHD
A First-in-human Study of EPI-321 in Facioscapulohumeral Muscular Dystrophy
Clinical Trial of Mexiletine Hydrochloride for Spinal and Bulbar Muscular Atrophy
Enrolling by InvitationNCT07164937 ↗
Imaging and Gait Analysis in FSHD Patients
👨⚕️ Enzo Ricci, Fondazione Policlinico Universitario A. Gemelli, IRCCS📍 1 site📅 Started Nov 2024View details ↗
RecruitingNCT06911190 ↗
Ten Year Follow-up in FSHD: the FOCUS 3 Study
RecruitingNCT07409142 ↗
BetterLife FSHD: A Patient-driven Health and Research Platform
Phase 2 Open-label Extension Study of AOC 1020 in Participants with Facioscapulohumeral Muscular Dystrophy (FSHD)
A Placebo-controlled Study of Clenbuterol in Spinal and Bulbar Muscular Atrophy
👨⚕️ Gianni Sorarù, MD, Azienda Ospedale Università di Padova📍 1 site📅 Started Apr 2024View details ↗
Walking ANalysis Interest in Persons wiTh facioscapulohumEral Muscular Dystrophies
An 18-month Prospective Natural History Study to Gain Insight Into FSHD2 Pathophysiology and Disease Progression
Longitudinal Study on Diaframmatic Ultrasound in FSHD Patients
Clinical, Molecular and Imaging Biomarkers in Spinal and Bulbar Muscular Atrophy (SBMA)
👨⚕️ Christopher Grunseich, M.D., National Institute of Neurological Disorders and Stroke (NINDS)📍 1 site📅 Started Oct 2021View details ↗
RecruitingNCT04635891 ↗
Motor Outcomes to Validate Evaluations in FSHD (MOVE FSHD)
👨⚕️ Jeffrey Statland, MD, University of Kansas Medical Center📍 20 sites📅 Started Dec 2020View details ↗
RecruitingNCT03458832 ↗
Clinical Trial Readiness to Solve Barriers to Drug Development in FSHD
👨⚕️ Jeffrey Statland, MD, University of Kansas Medical Center📍 14 sites📅 Started Mar 2018View details ↗
Specified Drug-Use Survey of Leuprorelin Acetate Injection Kit 11.25 mg "All-Case Investigation: Spinal and Bulbar Muscular Atrophy (SBMA)"
RecruitingNCT05966038 ↗
ALS/MND Natural History Study Data Repository
RecruitingNCT04001582 ↗
The United Kingdom Facioscapulohumeral Muscular Dystrophy Patient Registry
👨⚕️ Chiara Marini-Bettolo, MD, PhD, John Walton Muscular Dystrophy Research Centre📍 1 site📅 Started May 2013View details ↗
RecruitingNCT04369209 ↗
A Registered Cohort Study on FSHD1
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