🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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2+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 2 of 2 recruiting trials for “x-linked-myotubular-myopathy-abnormal-genitalia-syndrome

Phase 1, PHASE2RecruitingNCT07052929

Study of ASP2957 in Male Participants With X-linked Myotubular Myopathy Who Need Ventilators

👨‍⚕️ Medical Director, Astellas Gene Therapies📍 3 sites📅 Started Dec 2025View details ↗
RecruitingNCT06581146

A Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Condition

👨‍⚕️ Medical Director, Astellas Gene Therapies📍 5 sites📅 Started May 2025View details ↗

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