🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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6+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 6 of 6 recruiting trials for “thyroid-hypoplasia

Phase 2Enrolling by InvitationNCT07393373

Open-Label, Long-Term, Extension Study of Infigratinib in Children With Hypochondroplasia

👨‍⚕️ QED Therapeutics SVP, Clinical Development, QED Therapeutics, a BridgeBio company📍 25 sites📅 Started Apr 2026View details ↗
Phase 2RecruitingNCT07126262

A Study of Vosoritide Versus Placebo in Children With Hypochondroplasia Aged 0 to < 36 Months

🏥 BioMarin Pharmaceutical📍 26 sites📅 Started Jul 2025View details ↗
Phase 3Enrolling by InvitationNCT07073014

Long-Term Extension Study of Vosoritide to Treat Children With Hypochondroplasia

🏥 BioMarin Pharmaceutical📍 23 sites📅 Started Jun 2025View details ↗
Phase 2, PHASE3Enrolling by InvitationNCT06873035

An Interventional Study of Infigratinib in Children With Hypochondroplasia

🏥 QED Therapeutics, a BridgeBio company📍 22 sites📅 Started Apr 2025View details ↗
RecruitingNCT06410976

Prospective Clinical Assessment Study in Children With Hypochondroplasia

🏥 QED Therapeutics, a BridgeBio company📍 25 sites📅 Started Jun 2024View details ↗
RecruitingNCT06212947

A Multicenter Multinational Observational Study of Children With Hypochondroplasia

👨‍⚕️ Medical Director, MD, BioMarin Pharmaceutical📍 43 sites📅 Started Nov 2023View details ↗

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