Showing 1 of 1 recruiting trials for “Sphingolipidosis”
RecruitingNCT04885179 ↗
SPL Insufficiency Syndrome (SPLIS)/NPHS14: a SPLIS Observational Study and Patient Registry (International)
👨⚕️ Julie D Saba, MD, PhD, University of California, San Francisco📍 1 site📅 Started Apr 2025View details ↗
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