🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

Find Clinical Trials for Your Rare Disease

104+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

Clinical trial records are synced from ClinicalTrials.gov.
Report missing data
Clear

Showing 20 of 104 recruiting trials for “sickle-cell-beta-thalassemia-disease

RecruitingNCT07392216

Functional Ovarian Reserve in Sickle Cell Disease

👨‍⚕️ Christine Yu, MD, St. Jude Children's Research Hospital📍 1 site📅 Started Apr 2026View details ↗
Phase 4RecruitingNCT06979492

Prophylactic Transfusion In Pregnant in Women With Sickle Cell Disease

👨‍⚕️ Ross Fasano, MD, Emory University📍 1 site📅 Started Apr 2026View details ↗
NARecruitingNCT07246265

Morphine Clearance and Glomerular Filtration in Sickle Cell Patients in Crisis in Intensive Care

🏥 University Hospital, Tours📍 6 sites📅 Started Mar 2026View details ↗
RecruitingNCT07215975

A Real-World Study to Evaluate Luspatercept in Adults With Transfusion-Dependent Beta-Thalassemia in the Middle East

👨‍⚕️ Bristol Myers Squibb, Bristol-Myers Squibb📍 2 sites📅 Started Feb 2026View details ↗
Phase 1, PHASE2RecruitingNCT07432867

Efficacy Safety Study of Gene Therapy for Sickle Cell DiseaseSCD Using Autologous CD34+ Cells Transduced ex Vivo, Carrying a Corrected Globin Gene and a Silencing RNA.

👨‍⚕️ Elisa MAGRIN, PhD, Department of Biotherapy, Necker-Enfants Malades Hospital📍 1 site📅 Started Feb 2026View details ↗
NARecruitingNCT07222475

Writing Relaxing Beats in Adolescents Who Have Sickle Cell Disease

👨‍⚕️ C. Robert Bennett, PhD, Mayo Clinic📍 1 site📅 Started Feb 2026View details ↗
Phase 2RecruitingNCT07224360

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)

👨‍⚕️ Study Director, CSL Behring📍 3 sites📅 Started Feb 2026View details ↗
Phase 3RecruitingNCT07247188

Study of a Single Dose of a 21-valent Pneumococcal Conjugate Vaccine in Children and Adolescents With Sickle Cell Disease

👨‍⚕️ Clinical Sciences & Operations Study Director, Sanofi📍 1 site📅 Started Jan 2026View details ↗
NARecruitingNCT06919224

Delivering Patient-Facing Evidence-Based Guidelines Through mHealth to Adults With Sickle Cell Disease

👨‍⚕️ Robert M Cronin, MD, MS, Ohio State University📍 4 sites📅 Started Jan 2026View details ↗
Phase 1RecruitingNCT07187973

A Phase 1b, Open-Label Study of DISC-3405 in Participants With Sickle Cell Disease (SCD)

🏥 Disc Medicine, Inc📍 3 sites📅 Started Jan 2026View details ↗
Phase 1RecruitingNCT07431398

Single-dose Pharmacokinetics of Pociredir in Participants With Sickle Cell Disease

🏥 Fulcrum Therapeutics📍 6 sites📅 Started Dec 2025View details ↗
Phase 1RecruitingNCT07226219

Methylphenidate to Address Attention and Executive Deficits Among Children With Sickle Cell Disease

👨‍⚕️ Andrew Heitzer, PhD, St. Jude Children's Research Hospital📍 1 site📅 Started Nov 2025View details ↗
Enrolling by InvitationNCT07055503

Use of the Hemanext One® Hypoxic Red Blood Cell Storage System for Transfusion in Thalassemia Patients

👨‍⚕️ Antonis Kattamis, Professor, National and Kapodistrian University of Athens📍 1 site📅 Started Nov 2025View details ↗
Phase 2RecruitingNCT07023666

Early Screening and Treatment of Heart Complication in Sickle Cell Disease

👨‍⚕️ Sheinei Alan, MD, Inova Fairfax Hospital📍 2 sites📅 Started Oct 2025View details ↗
NARecruitingNCT07207577

Evaluation of Physiological and Psychological Factors Involved in Exercise Intolerance in Patients With β-TTD

👨‍⚕️ Laurent MESSONNIER, Université Savoie Mont Blanc📍 1 site📅 Started Sep 2025View details ↗
NARecruitingNCT06725550

Integrative Medicine in Pain Management in Sickle Cell Disease, 2.0

🏥 Indiana University📍 1 site📅 Started Aug 2025View details ↗
NARecruitingNCT06619197

Exploratory Study on Global Reflexology in Sickle Cell Disease

👨‍⚕️ COLLOT SOPHIE, Hospices Civils de Lyon📍 1 site📅 Started Jun 2025View details ↗
Phase 4RecruitingNCT06665997

Clinical and Biomarker Effects of Depot Medroxyprogesterone Acetate in Females With Sickle Cell Disease

👨‍⚕️ Andrea Roe, MD MPH, University of Pennsylvania📍 2 sites📅 Started Jun 2025View details ↗
Enrolling by InvitationNCT06717932

A Follow-up Study to Evaluate the Long-term Safety and Efficacy in Participants Who Received CS-101 Injection

🏥 CorrectSequence Therapeutics Co., Ltd📍 1 site📅 Started May 2025View details ↗
Phase 1, PHASE2RecruitingNCT06364774

ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia

👨‍⚕️ Janet Kwiatkowski, MD, Children's Hospital of Philadelphia📍 1 site📅 Started Apr 2025View details ↗
Page 1 of 6Next →

Get alerts when new trials open

Create a free account to follow conditions and receive trial notifications.

Create free account →