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Showing 20 of 34 recruiting trials for “rare-hypercholesterolemia

NARecruitingNCT07470723

The ORIGIN-FH Study

👨‍⚕️ Amy Peterson, MD, MS, University of Wisconsin, Madison📍 1 site📅 Started Feb 2026View details ↗
Phase 2RecruitingNCT07489209

A Dose-exploration Study of EDP167 in HoFH

👨‍⚕️ Kefei Dou, MD, Chinese Academy of Medical Sciences, Fuwai Hospital📍 1 site📅 Started Feb 2026View details ↗
NARecruitingNCT06960902

Study of the Determinants of Coronary Atherosclerosis in Familial Hypercholesterolemia (ATHERO-FH Study)

👨‍⚕️ Bertrand CARIOU, Pr📍 9 sites📅 Started Sep 2025View details ↗
Phase 2, PHASE3RecruitingNCT07058077

A Study of Enlicitide Decanoate (MK-0616, an Oral PCSK9 Inhibitor) in Children and Adolescents With Heterozygous Familial Hypercholesterolemia (MK-0616-029)

👨‍⚕️ Medical Director, Merck Sharp & Dohme LLC📍 21 sites📅 Started Aug 2025View details ↗
Phase 3RecruitingNCT07037771

A Phase 3 Study of Zodasiran in Adolescent and Adult Subjects With Homozygous Familial Hypercholesterolemia (YOSEMITE)

🏥 Arrowhead Pharmaceuticals📍 22 sites📅 Started Jun 2025View details ↗
RecruitingNCT06958315

Inclisiran (Leqvio®) in Patients With Atherosclerotic Vascular Disease and/or Heterozygous Familial Hypercholesterolemia Treated in Spain: the INSPIRE Study

🏥 Novartis Pharmaceuticals📍 19 sites📅 Started Jun 2025View details ↗
NARecruitingNCT06743659

Computerized Decision Support for Identification and Management of Familial Hypercholesterolemia

🏥 Brigham and Women's Hospital📍 1 site📅 Started Apr 2025View details ↗
RecruitingNCT04529967

Child-Parent Familial Hypercholesterolemia Screening

👨‍⚕️ LIling Qian, Master, Children's Hospital of Fudan University📍 6 sites📅 Started Apr 2025View details ↗
Phase 3RecruitingNCT06597006

Study to Evaluate Safety, Tolerability and Efficacy of Inclisiran in Children With Homozygous Familial Hypercholesterolemia

👨‍⚕️ Novartis Pharmaceuticals, Novartis Pharmaceuticals📍 18 sites📅 Started Feb 2025View details ↗
RecruitingNCT06634160

Assessment of the Prevalence of Steatotic Liver Disease Associated With Metabolic Dysfunction in Patients With Heterozygous Familial Hypercholesterolemia

🏥 Nantes University Hospital📍 3 sites📅 Started Jan 2025View details ↗
Phase 3RecruitingNCT06597019

Study to Evaluate Efficacy and Safety of Inclisiran in Children With Heterozygous Familial Hypercholesterolemia

👨‍⚕️ Novartis Pharmaceuticals, Novartis Pharmaceuticals📍 66 sites📅 Started Dec 2024View details ↗
NARecruitingNCT06331195

An Adapted Brazilian Cardioprotective Diet, Phytosterols and Krill Oil in Familial Hypercholesterolemia (DICA-FH)

👨‍⚕️ Aline Marcadenti, PhD, Hospital do Coracao📍 24 sites📅 Started Oct 2024View details ↗
NARecruitingNCT06439654

Atlantic Lipid Lowering Treatment Optimization Program

👨‍⚕️ Robert D Fishberg, MD, Atlantic Health System📍 2 sites📅 Started Jul 2024View details ↗
Enrolling by InvitationNCT06112327

Long-term Follow-up of Participants Dosed with an Investigational Gene Editing Therapy for Cardiovascular Disease

🏥 Verve Therapeutics, Inc.📍 3 sites📅 Started Jun 2024View details ↗
EARLY_Phase 1RecruitingNCT06458010

Clinical Exploration Trial of YOLT-101 in the Treatment of Familial Hypercholesterolemia (FH)

🏥 RenJi Hospital📍 1 site📅 Started May 2024View details ↗
Phase 1RecruitingNCT06164730

A Study of VERVE-102 in Patients With Familial Hypercholesterolemia or Premature Coronary Artery Disease

🏥 Verve Therapeutics, Inc.📍 21 sites📅 Started Apr 2024View details ↗
EARLY_Phase 1RecruitingNCT06461702

Clinical Exploration Trial of YOLT-101 in the Treatment of Familial Hypercholesterolemia (FH)

🏥 The First Affiliated Hospital of Bengbu Medical University📍 1 site📅 Started Apr 2024View details ↗
Phase 2RecruitingNCT04941599

2-Hydroxybenzylamine (2-HOBA) to Reduce HDL Modification and Improve HDL Function in Familial Hypercholesterolemia (FH)

👨‍⚕️ MacRae F. Linton, MD, Vanderbilt University Medical Center📍 1 site📅 Started Feb 2024View details ↗
NARecruitingNCT05614219

Familial Hypercholesterolemia Interpretive Comment - Nudging to Detection.

👨‍⚕️ Finn Lund Henriksen, Ph.d., Departement of Cardiology, Odense University Hospital📍 2 sites📅 Started Dec 2023View details ↗
EARLY_Phase 1RecruitingNCT06125847

NGGT006 Gene Therapy for Homozygous Familial Hypercholesterolemia

👨‍⚕️ Zuyi Yuan, M.D., First Affiliated Hospital of Xian Jiaotong University📍 1 site📅 Started Oct 2023View details ↗
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