Showing 20 of 22 recruiting trials for “peroxisomal-disease”
Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease
A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late Onset Pompe Disease (PROGRESS-GT LOPD)
Enrolling by InvitationNCT07212764 ↗
Mobile App-Based Infection Monitoring in Familial Mediterranean Fever
Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
Comparing Structured Neuromuscular Exercise and Exergaming Program in Adolescents With Familial Mediterranean Fever
Outcomes of Inspiratory Muscle Training in FMF Adolescents
Mediterranean Diet in Familial Mediterranean Fever: Is Fatty Liver Affected by Addition of Aerobic Exercise
is There an Effect of Adding Body Vibration to Intake of Vitamin D on Some Outcomes of Familial Mediterranean Fever
China Post-approval Commitment (PAC) Study of Avalglucosidase Alfa in Participants With IOPD
👨⚕️ Trial Transparency email recommended (Toll free for US & Canada)📍 1 site📅 Started May 2025View details ↗
RecruitingNCT06795152 ↗
Rare Glycogen Storage Diseases Natural History Study
RecruitingNCT06338891 ↗
Can Gluten/Wheat or Other Foods be Responsible for FMF Attacks
Evaluation of the Safety and Efficacy of Late-onset Pompe Disease Gene Therapy Drug
RecruitingNCT06121011 ↗
A Global Prospective Observational Registry of Patients With Pompe Disease
A Study to Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase Alfa/Miglustat in IOPD Subjects Aged 0 to <18
Safety and Efficacy of RPH-104 Used to Prevent Recurrent Fever Attacks in Adult Patients With Colchicine Resistant or Colchicine Intolerant Familial Mediterranean Fever
RecruitingNCT04478409 ↗
Characterization of a Functional Test for Mediterranean Family Fever Screening - 2
RecruitingNCT03564561 ↗
Natural History of Pompe Disease
RecruitingNCT07077473 ↗
Observing the Efficacy and Safety of Different Drugs Used in Real-world Familial Mediterranean Fever (FMF) Cases
RecruitingNCT04639336 ↗
Cognitive and Neurological Pathologies in Pompe Disease
RecruitingNCT01665326 ↗
Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease
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