🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

Find Clinical Trials for Your Rare Disease

22+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

ℹ
Clinical trial records are synced from ClinicalTrials.gov.
Report missing data
Clear

Showing 20 of 22 recruiting trials for “obsolete-alpha-1-antichymotrypsin-deficiency”

Phase 1RecruitingNCT07431112 ↗

A Study of AIR-001 in Adults With Alpha-1 Antitrypsin Deficiency (AATD)

👨‍⚕️ Clinical Information, AIRNA Corporation📍 2 sites📅 Started Feb 2026View details ↗
Phase 4RecruitingNCT07135427 ↗

Genetic Variation in IgG in Alpha 1 Antitrypsin Deficiency

🏥 University of Alabama at Birmingham📍 1 site📅 Started Sep 2025View details ↗
RecruitingNCT07152834 ↗

Screening for Alpha-1 Antitrypsin Deficiency in Patients With Airway Obstruction

🏥 Muğla Sıtkı Koçman University📍 1 site📅 Started Aug 2025View details ↗
RecruitingNCT06505603 ↗

PiMZ Longitudinal Cohort (PiMZ Logic)

👨‍⚕️ Monica Goldklang, MD, Columbia University📍 5 sites📅 Started May 2025View details ↗
Phase 1RecruitingNCT06996756 ↗

Gene Therapy for Alpha 1- Antitrypsin Deficiency

👨‍⚕️ Ronald G Crystal, MD, Weill Medical College of Cornell University📍 1 site📅 Started Feb 2025View details ↗
Phase 1RecruitingNCT06738017 ↗

Study of BMN 349 Single Dose in PiZZ and PiMZ/MASH Adult Participants

👨‍⚕️ Medical Director, MD, BioMarin Pharmaceutical📍 8 sites📅 Started Feb 2025View details ↗
NAEnrolling by InvitationNCT06892236 ↗

Preparation of IPSC for Cell Gene Editing for the Treatment of AATD

🏥 Fondazione IRCCS Policlinico San Matteo di Pavia📍 1 site📅 Started Jan 2025View details ↗
RecruitingNCT06512454 ↗

A Study in Adults to Learn About Inherited Alpha-1 Antitrypsin Deficiency (AATD) and AATD Related Liver Problems

👨‍⚕️ Study Director, Takeda📍 2 sites📅 Started Sep 2024View details ↗
Phase 1, PHASE2RecruitingNCT06405633 ↗

A Phase 1b/2a, Open-label Single Ascending Doses and Multiple Ascending Doses Study in Participants With Pi*ZZ AATD

👨‍⚕️ Cynthia Caracta, MD, Wave Life Sciences📍 9 sites📅 Started Jul 2024View details ↗
Phase 2RecruitingNCT05897424 ↗

Long-term, Open-label Study of SAR447537 (INBRX-101) in Adults With Alpha-1 Antitrypsin Deficiency Emphysema

👨‍⚕️ Clinical Sciences & Operations, Sanofi📍 40 sites📅 Started Jun 2024View details ↗
Phase 1, PHASE2RecruitingNCT06389877 ↗

A Study to Evaluate the Safety and Efficacy of BEAM-302 in Adult Patients With Alpha-1 Antitrypsin Deficiency (AATD)

👨‍⚕️ Medical Information, Beam Therapeutics📍 11 sites📅 Started Jun 2024View details ↗
Phase 3RecruitingNCT06165341 ↗

Study to Learn About the Safety of Fazirsiran and if it Can Help People With Alpha-1 Antitrypsin Liver Disease With Mild Liver Scarring (Fibrosis)

👨‍⚕️ Study Director, Takeda📍 41 sites📅 Started Mar 2024View details ↗
Phase 1RecruitingNCT06049082 ↗

A Study of KB408 for the Treatment of Alpha-1 Antitrypsin Deficiency

👨‍⚕️ David Sweet, MD, PhD, Director of Clinical Development📍 3 sites📅 Started Feb 2024View details ↗
Phase 3RecruitingNCT05677971 ↗

Study to Check the Safety of Fazirsiran and Learn if Fazirsiran Can Help People With Liver Disease and Scarring (Fibrosis) Due to an Abnormal Version of Alpha-1 Antitrypsin Protein

👨‍⚕️ Study Director, Takeda📍 89 sites📅 Started Mar 2023View details ↗
Phase 3RecruitingNCT04204252 ↗

Phase III, Efficacy and Safety of "Kamada-AAT for Inhalation"

👨‍⚕️ Jan Stolk, Prof, LUMC📍 9 sites📅 Started Nov 2019View details ↗
RecruitingNCT04157049 ↗

Alpha-1 Research Registry

🏥 Alpha-1 Foundation📍 1 site📅 Started Jun 2019View details ↗
NARecruitingNCT03455686 ↗

Exploring the Utility of Hyperpolarized 129Xe MRI in Healthy Volunteers and Patients With Lung Disease

👨‍⚕️ Parameswaran Nair, MD, PhD, McMaster University📍 1 site📅 Started Apr 2018View details ↗
RecruitingNCT05178277 ↗

Czech AATD Registry

👨‍⚕️ Jan MD Chlumsky, PhD, Thomayer University Hospital📍 1 site📅 Started Jan 2018View details ↗
Phase 3Enrolling by InvitationNCT02796937 ↗

Long Term Safety of Alpha1-Proteinase Inhibitor in Subjects With Alpha1 Antitrypsin Deficiency

🏥 Grifols Therapeutics LLC📍 28 sites📅 Started Jul 2016View details ↗
NARecruitingNCT01851642 ↗

Lung Disease and Its Affect on the Work of White Blood Cells in the Lungs

👨‍⚕️ Karina Serban, MD, University of Florida, College of Medicine, Division of Pulmonary, Critical Care, and Sleep Medicine📍 1 site📅 Started Aug 2007View details ↗
Page 1 of 2Next →

Get alerts when new trials open

Create a free account to follow conditions and receive trial notifications.

Create free account →