🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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4+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 4 of 4 recruiting trials for “metachromatic-leukodystrophy-late-infantile-form

NARecruitingNCT07046338

Lentiviral Hematopoietic Stem Cell Gene Therapy for MLD

👨‍⚕️ Lung-Ji Chang, Ph.D📍 1 site📅 Started Jun 2025View details ↗
NARecruitingNCT03725670

Direct Lentiviral Injection Gene Therapy for MLD

👨‍⚕️ Lung-Ji Chang, Ph.D, Shenzhen Geno-Immune Medical Institute📍 1 site📅 Started May 2025View details ↗
RecruitingNCT04925349

Modeling Macrophages Activation Pattern in X-linked Adrenoleukodystrophy, Metachromatic Leukodystrophy and Adult Onset Leukoencephalopathy With Axonal Spheroids and Pigmented Glia

👨‍⚕️ Fanny MOCHEL, MCU-PH, Institut du Cerveau et de la Moëlle épinière📍 2 sites📅 Started Aug 2021View details ↗
RecruitingNCT03333200

Longitudinal Study of Neurodegenerative Disorders

🏥 University of Pittsburgh📍 1 site📅 Started Jan 2012View details ↗

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