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Showing 9 of 9 recruiting trials for “metachromatic-leukodystrophy-juvenile-form

NARecruitingNCT07046338

Lentiviral Hematopoietic Stem Cell Gene Therapy for MLD

👨‍⚕️ Lung-Ji Chang, Ph.D📍 1 site📅 Started Jun 2025View details ↗
NARecruitingNCT03725670

Direct Lentiviral Injection Gene Therapy for MLD

👨‍⚕️ Lung-Ji Chang, Ph.D, Shenzhen Geno-Immune Medical Institute📍 1 site📅 Started May 2025View details ↗
RecruitingNCT06190834

Relationship Between High-Density Lipoprotein Subtypes and Coronary Heart Disease Prognosis.

👨‍⚕️ Yu Geng, Beijing Tsinghua Changgeng Hospital📍 1 site📅 Started Dec 2023View details ↗
NARecruitingNCT05420064

An Intervention to Increase Genetic Testing in Families Who May Share a Gene Mutation Related to Cancer Risk and An Intervention to Help Patients and Their Primary Care Providers Stay Up-to-date About Uncertain Genetic Test Results

👨‍⚕️ Kenneth Offit, MD, MPH, Memorial Sloan Kettering Cancer Center📍 8 sites📅 Started Dec 2022View details ↗
RecruitingNCT05103969

Cohort of Tumors With POLE/D1 Mutation

👨‍⚕️ Rosine GUIMBAUD, PhD.MD, Fédération francophone de Cancérologie digestive📍 1 site📅 Started Oct 2021View details ↗
RecruitingNCT04925349

Modeling Macrophages Activation Pattern in X-linked Adrenoleukodystrophy, Metachromatic Leukodystrophy and Adult Onset Leukoencephalopathy With Axonal Spheroids and Pigmented Glia

👨‍⚕️ Fanny MOCHEL, MCU-PH, Institut du Cerveau et de la Moëlle épinière📍 2 sites📅 Started Aug 2021View details ↗
Enrolling by InvitationNCT04503213

A Study to Assess CSF1R-related Leukoencephalopathy After Stem Cell Transplantation

👨‍⚕️ Zbigniew K Wszolek, MD, Mayo Clinic📍 1 site📅 Started Jul 2020View details ↗
Phase 2RecruitingNCT03428802

Pembrolizumab in Treating Participants With Metastatic, Recurrent or Locally Advanced Cancer and Genomic Instability

👨‍⚕️ Eugenia Girda, MD, Rutgers Cancer Institute of New Jersey📍 2 sites📅 Started Mar 2018View details ↗
RecruitingNCT03333200

Longitudinal Study of Neurodegenerative Disorders

🏥 University of Pittsburgh📍 1 site📅 Started Jan 2012View details ↗

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