🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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7+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 7 of 7 recruiting trials for “lysosomal-glycogen-storage-disease”

RecruitingNCT07459582 ↗

Accuracy of Home Lactate Meter and Accu-chek Glucometer in Patients With Glycogen Storage Disease

👨‍⚕️ Malaya Mount, MS, RD, CDN, Connecticut Children's📍 1 site📅 Started Mar 2026View details ↗
NARecruitingNCT06852612 ↗

Dietary Treatment Strategies and Metabolic Control in Glycogen Storage Disease Type I

👨‍⚕️ Michel Hochuli, MD, PhD, Department of Diabetes, Endocrinology, Nutritional Medicine and Metabolism📍 1 site📅 Started Apr 2025View details ↗
RecruitingNCT06843330 ↗

Accuracy of Lactate Meter in GSDIa

🏥 Connecticut Children's Medical Center📍 1 site📅 Started Apr 2025View details ↗
Phase 1, PHASE2RecruitingNCT06735755 ↗

A Phase 1/2, Dose-Exploration Study to Evaluate the Safety and Efficacy of BEAM-301 in Patients With Glycogen Storage Disease Type Ia (GSDIa)

🏥 Beam Therapeutics Inc.📍 3 sites📅 Started Dec 2024View details ↗
RecruitingNCT06636383 ↗

Glycogen Storage Disease Type Ia (GSDIa) Disease Monitoring Program

👨‍⚕️ Medical Director, Ultragenyx Pharmaceuticals Inc.📍 19 sites📅 Started Nov 2024View details ↗
RecruitingNCT06396546 ↗

'Glycogen Storage Diseases (GSDs) in Indian Children- Establishing an Indian GSD (I-GSD) Registry'

👨‍⚕️ Dr Vikrant Sood, DM, Institute of Liver & Biliary Sciences📍 3 sites📅 Started May 2024View details ↗
RecruitingNCT04454216 ↗

GSD VI and GSD IX Natural History

👨‍⚕️ Priya Kishnani, MD, Duke University📍 1 site📅 Started Sep 2020View details ↗

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