🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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7+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 7 of 7 recruiting trials for “Leukodystrophy”

Phase 1, PHASE2Enrolling by InvitationNCT06369974 ↗

Single Participant Study of an Experimental ASO Treatment for TUBB4A-related Leukodystrophy

👨‍⚕️ Florian Eichler, MD, Massachusetts General Hospital📍 1 site📅 Started Sep 2024View details ↗
NARecruitingNCT06224413 ↗

A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel

👨‍⚕️ Kiran Bhirangi, MD, bluebird bio, Inc.📍 3 sites📅 Started Mar 2024View details ↗
Phase 3RecruitingNCT05819866 ↗

A Clinical Study to Assess the Efficacy and Safety of Leriglitazone in Adult Male Subjects With Cerebral Adrenoleukodystrophy

🏥 Minoryx Therapeutics, S.L.📍 13 sites📅 Started Jul 2023View details ↗
Phase 1, PHASE2RecruitingNCT05757141 ↗

An Open-Label Exploratory Study of Fosigotifator in Participants With Vanishing White Matter Disease

👨‍⚕️ ABBVIE INC., AbbVie📍 5 sites📅 Started Mar 2023View details ↗
NARecruitingNCT03047369 ↗

The Myelin Disorders Biorepository Project

👨‍⚕️ Adeline Vanderver, MD, Children's Hospital of Philadelphia📍 20 sites📅 Started Dec 2016View details ↗
Phase 1RecruitingNCT02254863 ↗

UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

👨‍⚕️ Joanne Kurtzberg, MD, Duke University📍 1 site📅 Started Sep 2014View details ↗
RecruitingNCT03639285 ↗

Natural History, Diagnosis, and Outcomes for Leukodystrophies

🏥 University of Utah📍 1 site📅 Started Jan 2007View details ↗

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