🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

Find Clinical Trials for Your Rare Disease

3+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

Clinical trial records are synced from ClinicalTrials.gov.
Report missing data
Clear

Showing 3 of 3 recruiting trials for “l-ferritin-deficiency

EARLY_Phase 1RecruitingNCT07371767

CS-121 APOC3 Base Editing in Children and Adolescents With Hyperchylomicronemia

🏥 Shanghai Jiao Tong University School of Medicine📍 1 site📅 Started Jan 2026View details ↗
EARLY_Phase 1RecruitingNCT07176923

CS-121 APOC3 Base Editing in FCS

👨‍⚕️ YALIANG LI, CorrectSequence Therapeutics (Shanghai) Co., Ltd📍 1 site📅 Started Oct 2025View details ↗
NARecruitingNCT04227678

Postprandial Fatty Acid Metabolism in Subjects With Lipoprotein Lipase Deficiency

👨‍⚕️ André Carpentier, Université de Sherbrooke📍 1 site📅 Started Dec 2019View details ↗

Get alerts when new trials open

Create a free account to follow conditions and receive trial notifications.

Create free account →