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10+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 10 of 10 recruiting trials for “isolated-adrenal-medullary-hyperplasia

Phase 2, PHASE3RecruitingNCT07159841

A Study in Pediatric Participants With Congenital Adrenal Hyperplasia (Balance-CAH)

🏥 Crinetics Pharmaceuticals Inc.📍 18 sites📅 Started Jan 2026View details ↗
Phase 3RecruitingNCT07144163

A Study to Evaluate Atumelnant in Adults With Congenital Adrenal Hyperplasia

🏥 Crinetics Pharmaceuticals Inc.📍 17 sites📅 Started Dec 2025View details ↗
Phase 2RecruitingNCT07187375

Pharmacokinetics, Safety and Tolerability of Crinecerfont in Participants With Congenital Adrenal Hyperplasia Who Are Less Than 2 Years Old

🏥 Neurocrine Biosciences📍 3 sites📅 Started Sep 2025View details ↗
NARecruitingNCT07473804

Syndromes With Neonatal Salt Loss: Not Only Congenital Adrenal Hyperplasia Due to 21-hydroxylase Deficiency (21OH-ISC)

👨‍⚕️ Federico Baronio📍 1 site📅 Started Apr 2025View details ↗
Phase 2RecruitingNCT06712823

An Extension Study to Evaluate Safety and Efficacy in Participants Treated With CRN04894

🏥 Crinetics Pharmaceuticals Inc.📍 9 sites📅 Started Feb 2025View details ↗
NARecruitingNCT07099456

Fertility And Sexual Function In CAH: CALLIOPE

👨‍⚕️ Andrea M Isidori, MD, PhD, FRCP📍 1 site📅 Started Nov 2024View details ↗
Phase 1, PHASE2RecruitingNCT05669950

A Trial of Lu AG13909 in Participants With Congenital Adrenal Hyperplasia

👨‍⚕️ Email contact via H. Lundbeck A/S, HQ_Medinfo@Lundbeck.com📍 17 sites📅 Started Dec 2022View details ↗
RecruitingNCT06754423

Electronic Registry of Male Patients With Congenital Adrenal Hyperplasia 21-hydroxylase Deficiency

👨‍⚕️ Alessandra Gambineri, MD, IRCCS Azienda Ospedaliero-Universitaria di Bologna📍 1 site📅 Started Jun 2022View details ↗
Phase 4RecruitingNCT03760835

Congenital Adrenal Hyperplasia Once Daily Hydrocortisone Treatment

🏥 Federico II University📍 1 site📅 Started Aug 2016View details ↗
RecruitingNCT00250159

Natural History Study of Patients With Excess Androgen

👨‍⚕️ Deborah P Merke, M.D., Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)📍 2 sites📅 Started Jan 2006View details ↗

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