Showing 5 of 5 recruiting trials for “gm2-gangliosidosis-ab-variant”
A Study to Evaluate the Safety and Efficacy of Nizubaglustat (AZ-3102) in Patients With GM2 Gangliosidosis or Niemann-Pick Type C Disease
A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of GM1 Gangliosidosis or GM2 Gangliosidosis
RecruitingNCT05007990 ↗
Caregiving Networks Across Disease Context and the Life Course
👨⚕️ Laura M Koehly, Ph.D., National Human Genome Research Institute (NHGRI)📍 1 site📅 Started Sep 2022View details ↗
A Phase 1/2 Study of Intravenous Gene Transfer With an AAV9 Vector Expressing Human Beta-galactosidase in Type I and Type II GM1 Gangliosidosis
👨⚕️ Cynthia J Tifft, M.D., National Human Genome Research Institute (NHGRI)📍 1 site📅 Started Aug 2019View details ↗
RecruitingNCT00668187 ↗
A Natural History Study of the Gangliosidoses
👨⚕️ Jeanine R. Jarnes, PharmD, University of Minnesota - Fairview📍 1 site📅 Started Dec 2010View details ↗
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