🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

Find Clinical Trials for Your Rare Disease

2+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

ℹ
Clinical trial records are synced from ClinicalTrials.gov.
Report missing data
Clear

Showing 2 of 2 recruiting trials for “glycogen-storage-disease-due-to-phosphoglucomutase-deficiency”

Phase 1, PHASE2RecruitingNCT06735755 ↗

A Phase 1/2, Dose-Exploration Study to Evaluate the Safety and Efficacy of BEAM-301 in Patients With Glycogen Storage Disease Type Ia (GSDIa)

🏥 Beam Therapeutics Inc.📍 3 sites📅 Started Dec 2024View details ↗
RecruitingNCT06636383 ↗

Glycogen Storage Disease Type Ia (GSDIa) Disease Monitoring Program

👨‍⚕️ Medical Director, Ultragenyx Pharmaceuticals Inc.📍 19 sites📅 Started Nov 2024View details ↗

Get alerts when new trials open

Create a free account to follow conditions and receive trial notifications.

Create free account →