🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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5+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 5 of 5 recruiting trials for “blount-disease

Phase 1, PHASE2RecruitingNCT07185256

Safety and Tolerability of Subretinally Injected OPGx-BEST1 in Patients With Best Vitelliform Macular Dystrophy (BVMD) or Autosomal-Recessive Bestrophinopathy (ARB)

🏥 Opus Genetics, Inc📍 4 sites📅 Started Sep 2025View details ↗
RecruitingNCT06805474

A Prospective Observational Study to Assess the Reliability and Validity of the MLSDT

👨‍⚕️ Samuel Barone, MD, Nanoscope Therapeutics Inc.📍 1 site📅 Started Jan 2025View details ↗
RecruitingNCT06451575

Thrombophilia and Thrombosis in Behçet's Disease

👨‍⚕️ ERDAL PALA, Ataturk University📍 1 site📅 Started Jun 2023View details ↗
Phase 3RecruitingNCT04528082

Apremilast Pediatric Study in Children With Active Oral Ulcers Associated With Behçet's Disease

👨‍⚕️ MD, Amgen📍 27 sites📅 Started Sep 2021View details ↗
RecruitingNCT05809635

Study of BEST1 Vitelliform Macular Dystrophy

👨‍⚕️ Stephen H Tsang, MD, PhD, Columbia University📍 3 sites📅 Started Mar 2021View details ↗

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