🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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8+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 8 of 8 recruiting trials for “best-vitelliform-macular-dystrophy

Phase 1, PHASE2RecruitingNCT07185256

Safety and Tolerability of Subretinally Injected OPGx-BEST1 in Patients With Best Vitelliform Macular Dystrophy (BVMD) or Autosomal-Recessive Bestrophinopathy (ARB)

🏥 Opus Genetics, Inc📍 4 sites📅 Started Sep 2025View details ↗
RecruitingNCT06805474

A Prospective Observational Study to Assess the Reliability and Validity of the MLSDT

👨‍⚕️ Samuel Barone, MD, Nanoscope Therapeutics Inc.📍 1 site📅 Started Jan 2025View details ↗
Phase 2RecruitingNCT06290713

Vasodilator and Exercise Study for DMD (VASO-REx)

👨‍⚕️ Tanja Taivassalo, Ph.D., University of Florida, College of Medicine, Department of Physiology and Aging📍 1 site📅 Started Jun 2024View details ↗
Phase 2Enrolling by InvitationNCT06066580

Open-Label Extension of EDG-5506 in Participants With Becker Muscular Dystrophy

👨‍⚕️ Joanne M. Donovan, MD, PhD, Edgewise Therapeutics, Inc.📍 46 sites📅 Started Nov 2023View details ↗
RecruitingNCT05809635

Study of BEST1 Vitelliform Macular Dystrophy

👨‍⚕️ Stephen H Tsang, MD, PhD, Columbia University📍 3 sites📅 Started Mar 2021View details ↗
RecruitingNCT05019625

Biomarker Development for Muscular Dystrophies

👨‍⚕️ Thurman M. Wheeler, MD, Massachusetts General Hospital📍 5 sites📅 Started Feb 2015View details ↗
RecruitingNCT02069756

The Duchenne Registry

🏥 The Duchenne Registry📍 1 site📅 Started Oct 2007View details ↗
RecruitingNCT00390104

Molecular Analysis of Patients With Neuromuscular Disease

👨‍⚕️ Louis M Kunkel, PhD, Boston Children's Hospital/Harvard Medical School📍 1 site📅 Started Jan 2002View details ↗

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