🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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4+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 4 of 4 recruiting trials for “autosomal-dominant-omodysplasia

Phase 1RecruitingNCT06090669

Imatinib to Increase RUNX1 Activity in Participants With Germline RUNX1 Deficiency

👨‍⚕️ Lea C Cunningham, M.D., National Cancer Institute (NCI)📍 1 site📅 Started Dec 2023View details ↗
NARecruitingNCT04781790

French National Registry of Bone Marrow Failures

👨‍⚕️ Régis Peffault De Latour📍 1 site📅 Started Feb 2017View details ↗
NARecruitingNCT02958462

Pre-myeloid Cancer and Bone Marrow Failure Clinic Study

👨‍⚕️ Mrinal S. Patnaik, MBBS, Mayo Clinic📍 3 sites📅 Started Jan 2017View details ↗
RecruitingNCT01905826

Natural History Study of GATA2 Deficiency and Related Disorders

👨‍⚕️ Steven M Holland, M.D., National Institute of Allergy and Infectious Diseases (NIAID)📍 1 site📅 Started Aug 2013View details ↗

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