🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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7+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 7 of 7 recruiting trials for “atypical-rett-syndrome

Phase 4RecruitingNCT07308574

Post-Marketing Clinical Study of Ravulizumab in Participants With Clinical aHUS

🏥 Alexion Pharmaceuticals, Inc.📍 12 sites📅 Started Dec 2025View details ↗
NARecruitingNCT07218536

The Burden of Atypical Hemolytic Uremic Syndrome and The Clinical Characteristics of Patients in Egyptian Hospitals A Multicenter, Observational, Retrospective Cohort Study in Egypt

👨‍⚕️ AstraZeneca Clinical Study Information Center📍 8 sites📅 Started Oct 2025View details ↗
Phase 3RecruitingNCT05795140

Evaluate Long-term Safety, Tolerability and Efficacy of Iptacopan in Study Participants With aHUS

👨‍⚕️ Novartis Pharmaceuticals, Novartis Pharmaceuticals📍 6 sites📅 Started May 2024View details ↗
Phase 3RecruitingNCT05935215

Efficacy and Safety of Switching From Anti-C5 Antibody Treatment to Iptacopan Treatment in Study Participants With Atypical Hemolytic Uremic Syndrome (aHUS)

👨‍⚕️ Novartis Pharmaceuticals, Novartis Pharmaceuticals📍 31 sites📅 Started Feb 2024View details ↗
NARecruitingNCT05805202

Functional Implications of Rare Gene Mutations in aHUS Open the Door to Personalized Therapy

🏥 Mario Negri Institute for Pharmacological Research📍 1 site📅 Started May 2023View details ↗
RecruitingNCT04745195

Complement Prospective Evaluation of Thrombotic Microangiopathy on Endothelium

👨‍⚕️ Pieter van Paassen, MD, PhD, Maastricht University Medical Center📍 1 site📅 Started Aug 2021View details ↗
RecruitingNCT01522183

Atypical Hemolytic-Uremic Syndrome (aHUS) Registry

👨‍⚕️ Nuria Saval, Alexion Pharmaceuticals, Inc.📍 141 sites📅 Started Mar 2013View details ↗

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